{"id":1897,"date":"2022-08-07T20:58:54","date_gmt":"2022-08-07T11:58:54","guid":{"rendered":"https:\/\/1up-life.blog\/?p=1897"},"modified":"2022-08-07T20:58:54","modified_gmt":"2022-08-07T11:58:54","slug":"%e3%83%90%e3%83%bc%e3%83%86%e3%83%83%e3%82%af%e3%82%b9%e3%83%bb%e3%83%95%e3%82%a1%e3%83%bc%e3%83%9e%e3%82%b7%e3%83%a5%e3%83%bc%e3%83%86%e3%82%a3%e3%82%ab%e3%83%ab%e3%82%ba-vrtx2022%e5%b9%b4%e7%ac%ac","status":"publish","type":"post","link":"https:\/\/1up-life.blog\/?p=1897","title":{"rendered":"\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)2022\u5e74\u7b2c2\u56db\u534a\u671f\u6c7a\u7b97\u8aac\u660e\u4f1a"},"content":{"rendered":"<p>\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)2022\u5e74\u7b2c2\u56db\u534a\u671f\u6c7a\u7b97\u8aac\u660e\u4f1a\u306e\u65e5\u672c\u8a9e\u8a33\u3067\u3059\u3002<\/p>\n<p>\u58f2\u308a\u4e0a\u3052\u30fbEPS\u5171\u5e02\u5834\u4e88\u60f3\u3092\u4e0a\u56de\u3063\u3066\u304a\u308a\u30ac\u30a4\u30c0\u30f3\u30b9\u3082\u4e0a\u65b9\u4fee\u6b63\u3068\u826f\u3044\u611f\u3058\u3067\u3059\u306d\u3002<\/p>\n<p>\u4eca\u5f8c\u306f\u30d0\u30a4\u30aa\u95a2\u9023\u304c\u6ce8\u76ee\u3055\u308c\u308b\u3068\u3082\u8a00\u308f\u308c\u3066\u3044\u308b\u306e\u3067\u3053\u306e\u9298\u67c4\u306f\u6ce8\u76ee\u3057\u3066\u3044\u307e\u3059\u3002\u56a2\u80de\u6027\u7dda\u7dad\u75c7\u3067\u306f\u975e\u5e38\u306b\u826f\u3044\u85ac\u5264\u3092\u6301\u3063\u3066\u3044\u308b\u306e\u3067\u4eca\u5f8c\u3082\u5805\u8abf\u306b\u4f38\u3073\u308b\u3053\u3068\u3092\u671f\u5f85\u3057\u305f\u3044\u3067\u3059\u3002<\/p>\n<div id=\"attachment_1898\" style=\"width: 1489px\" class=\"wp-caption alignnone\"><img loading=\"lazy\" decoding=\"async\" aria-describedby=\"caption-attachment-1898\" class=\"wp-image-1898 size-full\" src=\"https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49.png\" alt=\"\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)\u682a\u4fa1\" width=\"1479\" height=\"816\" srcset=\"https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49.png 1479w, https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49-300x166.png 300w, https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49-1024x565.png 1024w, https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49-768x424.png 768w, https:\/\/1up-life.blog\/wp-content\/uploads\/2022\/08\/VRTX_2022-08-07_20-51-49-940x519.png 940w\" sizes=\"auto, (max-width: 1479px) 100vw, 1479px\" \/><p id=\"caption-attachment-1898\" class=\"wp-caption-text\">\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)\u682a\u4fa1<\/p><\/div>\n<p class=\"hh hh3 main-bdr\"><span class=\"big\"><strong>\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)2022\u5e74\u7b2c2\u56db\u534a\u671f\u6c7a\u7b97\u8aac\u660e\u4f1a<\/strong><\/span><\/p>\n<p>Call participants:<br \/>\nCharlie Wagner &#8212; Chief Financial Officer<br \/>\nReshma Kewalramani &#8212; Chief Executive Officer and President<br \/>\nStuart Arbuckle &#8212; Chief Operating Officer<br \/>\nSalveen Richter &#8212; Goldman Sachs &#8212; Analyst<br \/>\nMike Yee &#8212; Jefferies &#8212; Analyst<br \/>\nLyla Youssef &#8212; Cowen and Company &#8212; Analyst<br \/>\nLiisa Bayko &#8212; Evercore ISI &#8212; Analyst<br \/>\nGeoff Meacham &#8212; Bank of America Merrill Lynch &#8212; Analyst<br \/>\nEvan Seigerman &#8212; BMO Capital Markets &#8212; Analyst<br \/>\nColin Bristow &#8212; UBS &#8212; Analyst<br \/>\nDavid Risinger &#8212; SVB Securities &#8212; Analyst<br \/>\nMohit Bansal &#8212; Wells Fargo Securities &#8212; Analyst<br \/>\nOlivia Brayer &#8212; Cantor Fitzgerald &#8212; Analyst<br \/>\nHartaj Singh &#8212; Oppenheimer and Company &#8212; Analyst<br \/>\nBrian Abrahams &#8212; RBC Capital Markets &#8212; Analyst<br \/>\nMore VRTX analysis<\/p>\n<p>2022\u5e748\u67084\u65e5\u5348\u5f8c4\u664230\u5206<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba\u306e2022\u5e74\u7b2c2\u56db\u534a\u671f\u6c7a\u7b97\u8aac\u660e\u4f1a\u306b\u3088\u3046\u3053\u305d\u3002[\u30aa\u30da\u30ec\u30fc\u30bf\u30fc\u306e\u65b9\u3078\u3011\u3053\u306e\u30a4\u30d9\u30f3\u30c8\u306f\u9332\u97f3\u3055\u308c\u3066\u3044\u307e\u3059\u306e\u3067\u3054\u6ce8\u610f\u304f\u3060\u3055\u3044\u3002\u305d\u308c\u3067\u306f\u3001\u6700\u9ad8\u8ca1\u52d9\u8cac\u4efb\u8005\u306e\u30c1\u30e3\u30fc\u30ea\u30fc\u30fb\u30ef\u30b0\u30ca\u30fc\u3055\u3093\u306b\u4f1a\u8b70\u3092\u5f15\u304d\u7d99\u304e\u305f\u3044\u3068\u601d\u3044\u307e\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>\u30c1\u30e3\u30fc\u30ea\u30fc\u30fb\u30ef\u30b0\u30ca\u30fc &#8212; \u6700\u9ad8\u8ca1\u52d9\u8cac\u4efb\u8005<\/p>\n<p>\u3053\u3093\u3070\u3093\u306f\u3002\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u793e\u306e\u6700\u9ad8\u8ca1\u52d9\u8cac\u4efb\u8005\u3001\u30c1\u30e3\u30fc\u30ea\u30fc\u30fb\u30ef\u30b0\u30ca\u30fc\u3067\u3059\u30022022 \u5e74\u7b2c 2 \u56db\u534a\u671f\u6c7a\u7b97\u306e\u96fb\u8a71\u4f1a\u8b70\u306b\u3088\u3046\u3053\u305d\u3002\u4eca\u591c\u306e\u96fb\u8a71\u3067\u306f\u3001\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u306eCEO\u517c\u793e\u9577\u3067\u3042\u308bReshma Kewalramani\u535a\u58eb\u3001\u6700\u9ad8\u57f7\u884c\u8cac\u4efb\u8005\u306eStuart 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Kewalramani\u535a\u58eb\u306b\u96fb\u8a71\u3092\u3064\u306a\u304e\u307e\u3059\u3002<\/p>\n<p>\u30ec\u30b7\u30e5\u30de\u30fb\u30b1\u30ef\u30e9\u30de\u30fc\u30cb\u306b\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>\u30ec\u30b7\u30e5\u30de\u30fb\u30b1\u30ef\u30e9\u30de\u30fc\u30cb &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<br 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1\u304a\u3088\u3073SKYLINE 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GAAP \u30d9\u30fc\u30b9\uff09\u306f\u3001\u524d\u56de\u4e88\u60f3\u3057\u305f 28.2 \u5104\u30c9\u30eb\u304b\u3089 31 \u5104\u30c9\u30eb\u306b\u5897\u52a0\u3059\u308b\u898b\u8fbc\u307f\u3067\u3059\u3002\u3053\u306e\u5897\u52a0\u306f\u3001\u4e3b\u306b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u30fb\u30d7\u30ed\u30b0\u30e9\u30e0\u3001\u7279\u306b\u75bc\u75db\u9818\u57df\u3068AMKD\u306e\u5f8c\u671f\u81e8\u5e8a\u8a66\u9a13\u3078\u306e\u9032\u5c55\u306b\u4f34\u3046\u8cbb\u7528\u306e\u5897\u52a0\u3001\u306a\u3089\u3073\u306b\u8ffd\u52a0\u306e\u5951\u7d04\u4e00\u6642\u91d1\u3084\u30de\u30a4\u30eb\u30b9\u30c8\u30fc\u30f3\u652f\u6255\u306b\u3088\u308b\u3082\u306e\u3067\u3059\u3002\u6700\u5f8c\u306b\u3001\u975eGAAP\u30d9\u30fc\u30b9\u306e\u5b9f\u52b9\u7a0e\u7387\u306f\u3001\u5f15\u304d\u7d9a\u304d21\uff05\u304b\u308922\uff05\u306e\u7bc4\u56f2\u3068\u4e88\u60f3\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>2022\u5e74\u5f8c\u534a\u304b\u30892023\u5e74\u524d\u534a\u306b\u304b\u3051\u3066\u306f\u3001\u5f53\u793e\u306e\u7d99\u7d9a\u7684\u306a\u9032\u6b69\u3092\u793a\u3059\u91cd\u8981\u306a\u30de\u30a4\u30eb\u30b9\u30c8\u30fc\u30f3\u304c\u3044\u304f\u3064\u304b\u63a7\u3048\u3066\u3044\u307e\u3059\u3002\u5148\u307b\u3069Reshma\u304c\u8a71\u3057\u305f\u3088\u3046\u306b\u3001Vertex\u306f\u65b0\u305f\u306a\u5909\u66f2\u70b9\u3092\u8fce\u3048\u3066\u3044\u307e\u3059\u3002\u5f53\u793e\u306f8\u5e74\u9023\u7d9a\u30672\u6841\u306e\u53ce\u76ca\u6210\u9577\u7387\u3092\u9054\u6210\u3057\u3066\u304a\u308a\u3001\u4eca\u5f8c\u6570\u5e74\u306b\u308f\u305f\u308a\u5f37\u529b\u306a\u30ad\u30e3\u30c3\u30b7\u30e5\u30d5\u30ed\u30fc\u3092\u3082\u305f\u3089\u3059CF\u306e\u9577\u671f\u7684\u306a\u30ea\u30fc\u30c0\u30fc\u30b7\u30c3\u30d7\u306b\u3088\u308a\u3001\u6975\u3081\u3066\u8010\u4e45\u6027\u306e\u9ad8\u3044\u4e8b\u696d\u3092\u69cb\u7bc9\u3057\u3066\u3044\u307e\u3059\u3002\u307e\u305f\u3001\u4e8b\u696d\u306e\u591a\u69d8\u5316\u3082\u9806\u8abf\u306b\u9032\u3093\u3067\u304a\u308a\u30015\u3064\u306e\u75be\u60a3\u9818\u57df\u3067\u5f8c\u671f\u958b\u767a\u6bb5\u968e\u306b\u3042\u308a\u3001\u8907\u6570\u306e\u65b0\u85ac\u306e\u81e8\u5e8a\u5c0e\u5165\u304c\u4e88\u5b9a\u3055\u308c\u3066\u3044\u308b\u306a\u3069\u3001\u9577\u671f\u7684\u306a\u6210\u9577\u30dd\u30c6\u30f3\u30b7\u30e3\u30eb\u3092\u9ad8\u3081\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u79c1\u305f\u3061\u306f\u3001\u9769\u65b0\u7684\u3067\u9ad8\u4fa1\u5024\u306e\u533b\u85ac\u54c1\u3092\u751f\u307f\u51fa\u3059\u3053\u3068\u3092\u610f\u56f3\u3057\u3066\u3053\u308c\u3089\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u3092\u958b\u767a\u3057\u3066\u304a\u308a\u3001\u305d\u308c\u305e\u308c\u304c\u6570\u5341\u5104\u30c9\u30eb\u898f\u6a21\u306e\u30d3\u30b8\u30cd\u30b9\u30c1\u30e3\u30f3\u30b9\u3092\u8868\u3057\u3066\u3044\u307e\u3059\u3002CF\u306e\u6210\u529f\u306b\u5f8c\u62bc\u3057\u3055\u308c\u3001\u5f53\u793e\u306f\u524d\u9032\u3059\u308b\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306b\u6295\u8cc7\u3057\u7d9a\u3051\u308b\u3053\u3068\u304c\u3067\u304d\u308b\u3068\u540c\u6642\u306b\u3001\u512a\u308c\u305f\u53ce\u76ca\u6027\u3068\u30ad\u30e3\u30c3\u30b7\u30e5\u30d5\u30ed\u30fc\u3092\u5b9f\u73fe\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u307e\u3059\u3002\u672c\u5e74\u3082\u5f15\u304d\u7d9a\u304d\u3001\u5f53\u793e\u306e\u3055\u3089\u306a\u308b\u9032\u5c55\u3092\u304a\u4f1d\u3048\u3057\u3066\u307e\u3044\u308a\u307e\u3059\u306e\u3067\u3001\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3044\u305f\u3057\u307e\u3059\u3002\u305d\u308c\u3067\u306f\u3001\u8cea\u554f\u3092\u304a\u53d7\u3051\u3057\u307e\u3059\u3002<\/p>\n<p class=\"hh hh6 main-c main-bdr\"><span class=\"big\"><strong>\u8cea\u7591\u5fdc\u7b54<\/strong><\/span><\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002[\u30aa\u30da\u30ec\u30fc\u30bf\u30fc\u304b\u3089\u306e\u3054\u6848\u5185] \u305d\u308c\u3067\u306f\u6700\u521d\u306e\u8cea\u554f\u306f\u30b4\u30fc\u30eb\u30c9\u30de\u30f3\u30fb\u30b5\u30c3\u30af\u30b9\u306e\u30b5\u30eb\u30f4\u30a3\u30fc\u30f3\u30fb\u30ea\u30d2\u30bf\u30fc\u304b\u3089\u304a\u9858\u3044\u3057\u307e\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>\u30b5\u30eb\u30d3\u30fc\u30f3\u30fb\u30ea\u30d2\u30bf\u30fc &#8212; \u30b4\u30fc\u30eb\u30c9\u30de\u30f3\u30fb\u30b5\u30c3\u30af\u30b9 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3002\u79c1\u306e\u8cea\u554f\u306b\u7b54\u3048\u3066\u304f\u308c\u3066\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u7d20\u6674\u3089\u3057\u3044\u56db\u534a\u671f\u3067\u3057\u305f\u3002\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u8cea\u554f\u3067\u3059\u304c\u3001\u30d9\u30fc\u30bf\u7d30\u80de\u3068\u938c\u72b6\u8d64\u8840\u7403\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u3044\u3066\u3001FDA\u306f\u60a3\u8005\u6570\u306b\u95a2\u3057\u3066\u3069\u306e\u3088\u3046\u306a\u3053\u3068\u3092\u671b\u3093\u3067\u3044\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u307e\u305f\u3001\u305d\u306e\u671f\u9593\u3067\u3059\u304c\u3001\u30d6\u30eb\u30fc\u30d0\u30fc\u30c9\u3068\u540c\u3058\u3088\u3046\u306b2\u5e74\u4ee5\u5185\u306e\u5272\u5408\u3067\u898b\u3066\u3044\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u305d\u306e\u3042\u305f\u308a\u3092\u304a\u805e\u304b\u305b\u304f\u3060\u3055\u3044\u3002<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3001Salveen\u3055\u3093\u3001Reshma\u3067\u3059\u3002\u30a8\u30af\u30b5\u30bb\u30eb\u30fb\u30d7\u30ed\u30b0\u30e9\u30e0\u3068FDA\u304c\u6c42\u3081\u3066\u3044\u308b\u3082\u306e\u306b\u3064\u3044\u3066\u3067\u3059\u304c\u3001\u30d5\u30a1\u30a4\u30eb\u5185\u306e\u60a3\u8005\u6570\u3068\u30d5\u30a9\u30ed\u30fc\u30a2\u30c3\u30d7\u306e\u671f\u9593\u306b\u3064\u3044\u3066\u7d50\u8ad6\u3092\u51fa\u3059\u306b\u306f\u3001\u3053\u306e2\u3064\u306e\u9818\u57df\u306b\u7d5e\u3089\u308c\u307e\u3059\u3002\u79c1\u305f\u3061\u306f\u3001\u904e\u53bb\u4f55\u30ab\u6708\u306b\u3082\u308f\u305f\u3063\u3066FDA\u3068\u975e\u5e38\u306b\u751f\u7523\u7684\u306a\u8a71\u3057\u5408\u3044\u3092\u884c\u3063\u3066\u304d\u3066\u304a\u308a\u3001\u524d\u81e8\u5e8a\u30d1\u30c3\u30b1\u30fc\u30b8\u3001CMC\u3001\u88fd\u9020\u3001\u305d\u306e\u4ed6\u3059\u3079\u3066\u306e\u30e2\u30b8\u30e5\u30fc\u30eb\u306b\u95a2\u3059\u308b\u8a71\u3057\u5408\u3044\u306f\u7d42\u4e86\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u3053\u306e2\u3064\u306e\u9818\u57df\u306b\u3064\u3044\u3066\u3067\u3059\u3002\u4eca\u5f8c\u6570\u9031\u9593\u306e\u3046\u3061\u306b\u3001\u3053\u308c\u3089\u306e\u4f1a\u8a71\u3092\u7d42\u3048\u308b\u4e88\u5b9a\u3067\u3059\u3002\u3067\u3059\u304b\u3089\u3001\u79c1\u305f\u3061\u306f\u63a8\u6e2c\u3059\u308b\u5fc5\u8981\u306f\u3042\u308a\u307e\u305b\u3093\u3002\u305d\u306e\u5f8c\u3001\u307e\u305f\u3054\u5831\u544a\u3067\u304d\u308b\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>\u3057\u304b\u3057\u3001\u672c\u5f53\u306b\u3053\u306e2\u70b9\u3060\u3051\u306a\u306e\u3067\u3059\u3002\u30d5\u30a1\u30a4\u30eb\u5185\u306e\u60a3\u8005\u6570\u3001\u305d\u3057\u3066\u30d5\u30a9\u30ed\u30fc\u30a2\u30c3\u30d7\u306e\u671f\u9593\u3067\u3059\u3002\u79c1\u305f\u3061\u306f\u3001EMA\u3084MHRA\u3068\u540c\u3058\u3088\u3046\u306a\u30c6\u30fc\u30de\u3067\u8a71\u3092\u3057\u3066\u304d\u3066\u3001\u7d50\u8ad6\u306b\u81f3\u3063\u305f\u3068\u3044\u3046\u3053\u3068\u3092\u7e70\u308a\u8fd4\u3057\u307e\u3059\u3002<\/p>\n<p>\u53f8\u4f1a<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u3001\u30b8\u30a7\u30d5\u30ea\u30fc\u30ba\u306eMichael Yee\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Mike Yee &#8212; Jefferies &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3069\u3046\u3082\u3001\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u3053\u3093\u306b\u3061\u306f\u3002\u30a4\u30ca\u30af\u30b5\u30d7\u30ea\u30f3\u306b\u3064\u3044\u3066\u8cea\u554f\u3067\u3059\u3002\u7b2c2\u76f8\u306e\u767b\u9332\u304c\u5b8c\u4e86\u3057\u3001\u7b2c3\u76f8\u306b\u79fb\u884c\u3057\u3066\u3044\u307e\u3059\u306d\u3002<\/p>\n<p>\u7b2c2\u76f8\u306e\u767b\u9332\u304c\u3069\u306e\u3088\u3046\u306a\u30da\u30fc\u30b9\u3067\u9032\u3093\u3067\u3044\u308b\u306e\u304b\u3001\u307e\u305f\u3001\u5e74\u672b\u306b\u8a71\u3059\u3079\u304d\u30c7\u30fc\u30bf\u304c\u3042\u308b\u306e\u304b\u3001\u30b3\u30e1\u30f3\u30c8\u3044\u305f\u3060\u3051\u307e\u3059\u304b\uff1f\u767b\u9332\u304c\u56f0\u96e3\u306a\u4eba\u53e3\u5c64\u3067\u3042\u308b\u3053\u3068\u306f\u627f\u77e5\u3057\u3066\u3044\u307e\u3059\u306e\u3067\u3001\u305d\u308c\u304c\u7b2c3\u76f8\u3092\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u308b\u304b\u306e\u30d2\u30f3\u30c8\u306b\u306a\u308b\u3068\u601d\u3044\u307e\u3059\u3002\u305d\u308c\u306b\u3064\u3044\u3066\u5c11\u3057\u304a\u8a71\u3044\u305f\u3060\u3051\u307e\u3059\u304b\u3002\u305d\u308c\u304b\u3089\u3001Salveen\u306e\u30a8\u30af\u30b5\u30bb\u30eb\u306b\u95a2\u3059\u308b\u8cea\u554f\u3078\u306e\u88dc\u8db3\u3067\u3059\u3002\u3082\u30572\u5e74\u9593\u306e\u6295\u4e0e\u304c\u5fc5\u8981\u3060\u3068\u3057\u305f\u3089\u3001\u3069\u306e\u304f\u3089\u3044\u5148\u9001\u308a\u306b\u306a\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f1\u5e74\u5148\u9001\u308a\u306b\u306a\u308b\u306e\u3067\u3057\u3087\u3046\u304b\u3002\u3042\u308b\u3044\u306f\u3001\u305d\u306e\u8fba\u306e\u4e8b\u60c5\u306b\u3064\u3044\u3066\u6559\u3048\u3066\u304f\u3060\u3055\u3044\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u30de\u30a4\u30b1\u30eb\u3001\u8cea\u554f\u304c1\u3064\u3042\u308a\u307e\u3057\u305f\u306d\u3002\u4e00\u3064\u306fAMKD\u306b\u3064\u3044\u3066\u3001\u3082\u3046\u4e00\u3064\u306fexa-cel\u306b\u3064\u3044\u3066\u3067\u3059\u3002\u307e\u305a\u3001\u30a8\u30af\u30b5\u30bb\u30eb\u306b\u3064\u3044\u3066\u7de0\u3081\u62ec\u3089\u305b\u3066\u3044\u305f\u3060\u304d\u307e\u3059\u3002<\/p>\n<p>\u4eca\u304a\u8a71\u3057\u305f\u3088\u3046\u306b\u3001\u4eca\u5f8c\u6570\u9031\u9593\u306e\u3046\u3061\u306bFDA\u3068\u306e\u30df\u30fc\u30c6\u30a3\u30f3\u30b0\u3092\u884c\u3044\u3001\u3053\u306e\u8b70\u8ad6\u3092\u307e\u3068\u3081\u308b\u4e88\u5b9a\u3067\u3059\u3002\u305d\u306e\u305f\u3081\u3001\u79c1\u305f\u3061\u306f\u63a8\u6e2c\u3059\u308b\u5fc5\u8981\u306f\u306a\u3044\u3067\u3057\u3087\u3046\u3002\u8fd1\u3044\u5c06\u6765\u3001\u5177\u4f53\u7684\u306a\u5185\u5bb9\u3092\u304a\u77e5\u3089\u305b\u3057\u3001\u30b9\u30b1\u30b8\u30e5\u30fc\u30eb\u3092\u304a\u77e5\u3089\u305b\u3067\u304d\u308b\u3068\u601d\u3044\u307e\u3059\u3002AMKD\u306b\u3064\u3044\u3066\u306f\u3001\u60a3\u8005\u96c6\u56e3\u306b\u57fa\u3065\u304f\u767b\u9332\u306e\u96e3\u3057\u3055\u306b\u3064\u3044\u3066\u306e\u3054\u6307\u6458\u306f\u3001\u672c\u5f53\u306b\u826f\u3044\u3054\u6307\u6458\u3060\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>AMKD\u306e\u60a3\u8005\u5c64\u306fCF\u3068\u591a\u304f\u306e\u985e\u4f3c\u70b9\u304c\u3042\u308a\u307e\u3059\u304c\u3001\u907a\u4f1d\u7684\u8981\u56e0\u306b\u3088\u308b\u75be\u60a3\u3067\u3001\u7d0410\u4e07\u4eba\u306e\u60a3\u8005\u304c\u304a\u308a\u3001CF\u306e\u6cbb\u7642\u30a2\u30d7\u30ed\u30fc\u30c1\u306f\u3001\u75be\u60a3\u306e\u6839\u672c\u539f\u56e0\u3067\u3042\u308bCFTR\u30bf\u30f3\u30d1\u30af\u8cea\u3092\u6a19\u7684\u3068\u3059\u308b\u3053\u3068\u3067\u3059\u3002AMKD\u306e\u5834\u5408\u3082\u540c\u3058\u3067\u3059\u3002\u79c1\u305f\u3061\u306f\u3001APOL1\u30bf\u30f3\u30d1\u30af\u8cea\u3092\u6a19\u7684\u3068\u3057\u3066\u3044\u307e\u3059\u3002\u5927\u304d\u306a\u9055\u3044\u306f\u3001\u8a3a\u65ad\u3001\u75be\u60a3\u8a8d\u77e5\u3001\u907a\u4f1d\u5b50\u578b\u5224\u5b9a\u306b\u3042\u308a\u307e\u3059\u3002<\/p>\n<p>\u3057\u304b\u3057\u3001\u3053\u306e\u3053\u3068\u3092\u8a8d\u8b58\u3057\u305f\u4e0a\u3067\u3001\u79c1\u305f\u3061\u306f\u3053\u306e\u7b2c2\/3\u76f8\u30d7\u30ed\u30b0\u30e9\u30e0\u306b3\u3064\u306e\u30a4\u30cb\u30b7\u30a2\u30c1\u30d6\u3092\u5165\u308c\u307e\u3057\u305f\u30021\u3064\u76ee\u306f\u3001\u4e16\u754c\u5404\u5730\u306b150\u4ee5\u4e0a\u306e\u65bd\u8a2d\u3092\u958b\u8a2d\u3057\u3001\u60a3\u8005\u3055\u3093\u304c\u3044\u308b\u5834\u6240\u306e\u8fd1\u304f\u306b\u3001\u305d\u3057\u3066\u5358\u7d14\u306b\u591a\u304f\u306e\u60a3\u8005\u3055\u3093\u304c\u3044\u308b\u3088\u3046\u306b\u3059\u308b\u3053\u3068\u3067\u3059\u30022\u3064\u76ee\u306f\u3001\u73fe\u5728\u9032\u884c\u4e2d\u306e\u89b3\u5bdf\u7814\u7a76\u3067\u3059\u3002\u3053\u308c\u306f\u30b8\u30a7\u30ce\u30bf\u30a4\u30d4\u30f3\u30b0\u7814\u7a76\u3067\u3059\u3002<\/p>\n<p>APOL1\u306e\u5bfe\u7acb\u907a\u4f1d\u5b50\u304c2\u3064\u3042\u308b\u4eba\u306f\u3001\u7121\u4f5c\u70ba\u5316\u6bd4\u8f03\u8a66\u9a13\u306b\u767b\u9332\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u307e\u3059\u3002\u6700\u5f8c\u306b\u3001\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u304c\u8a71\u3057\u3066\u3044\u305f\u3088\u3046\u306b\u3001\u79c1\u305f\u3061\u306f\u60a3\u8005\u56e3\u4f53\u3084\u533b\u5e2b\u56e3\u4f53\u3001\u5730\u57df\u793e\u4f1a\u5168\u4f53\u3068\u5354\u529b\u3057\u3066\u3001\u610f\u8b58\u3092\u9ad8\u3081\u308b\u52aa\u529b\u3092\u3057\u3066\u3044\u307e\u3059\u3002\u30de\u30a4\u30b1\u30eb\u3001\u7b2c2\/3\u76f8\u8a66\u9a13\u306e\u512a\u308c\u305f\u70b9\u306f\u3001\u3059\u3079\u3066\u3092\u524d\u3082\u3063\u3066\u884c\u3046\u3053\u3068\u3067\u3059\u3002\u3064\u307e\u308a\u3001\u7b2c3\u76f8\u8a66\u9a13\u3068\u306a\u308b\u8a66\u9a13\u5834\u306f\u3001\u7b2c2\/3\u76f8\u8a66\u9a13\u306e\u4e00\u74b0\u3068\u3057\u3066\u3001\u73fe\u5728\u3059\u3079\u3066\u30aa\u30fc\u30d7\u30f3\u306b\u306a\u3063\u3066\u3044\u308b\u306e\u3067\u3059\u3002<\/p>\n<p>Mike Yee &#8212; \u30b8\u30a7\u30d5\u30ea\u30fc\u30ba &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u7b2c2\u76f8\u306e\u30c7\u30fc\u30bf\u63d0\u4f9b\u306f\u78ba\u7d04\u3055\u308c\u3066\u3044\u308b\u306e\u3067\u3059\u304b\uff1f\u4f55\u304b\u304a\u3063\u3057\u3083\u308b\u3053\u3068\u306f\u3042\u308a\u307e\u3059\u304b\u3001\u305d\u308c\u3068\u3082\u524d\u306b\u9032\u3080\u3060\u3051\u3067\u3059\u304b\uff1f<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u30c7\u30fc\u30bf\u306b\u3064\u3044\u3066\u306e\u3054\u8cea\u554f\u3067\u3057\u305f\u306d\u3002\u7b2c2\u76f8\u306e\u6295\u4e0e\u91cf\u3092\u6c7a\u5b9a\u3057\u305f\u6642\u70b9\u3067\u3001\u79c1\u305f\u3061\u304b\u3089\u306e\u9023\u7d61\u3092\u671f\u5f85\u3057\u3066\u3044\u3066\u304f\u3060\u3055\u3044\u3002<\/p>\n<p>Mike Yee &#8212; \u30b8\u30a7\u30d5\u30ea\u30fc\u30ba &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u308f\u304b\u308a\u307e\u3057\u305f\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u30b3\u30fc\u30a6\u30a7\u30f3\u306ePhil Nadeau\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Lyla Youssef &#8212; Cowen and Company &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3001\u30d5\u30a3\u30eb\u306b\u4ee3\u308f\u3063\u3066\u30e9\u30a4\u30e9\u3067\u3059\u3002\u8cea\u554f\u306b\u7b54\u3048\u3066\u304f\u308c\u3066\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002147\u306b\u3064\u3044\u3066\u3060\u3051\u3067\u3059\u304c\u3002<\/p>\n<p>\u53ef\u80fd\u3067\u3042\u308c\u3070\u3001\u7b2c2\/3\u76f8\u8a66\u9a13\u306b\u767b\u9332\u3055\u308c\u305f\u60a3\u8005\u306e\u6f5c\u5728\u7684\u306a\u57fa\u672c\u7279\u6027\u306b\u3064\u3044\u3066\u3001\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u3066\u3044\u308b\u304b\u3001\u6700\u65b0\u60c5\u5831\u3092\u6559\u3048\u3066\u304f\u3060\u3055\u3044\u3002\u30bf\u30f3\u30d1\u30af\u5c3f\u3084eGFR\u306e\u6f5c\u5728\u7684\u306a\u9055\u3044\u306b\u3064\u3044\u3066\u3001APOL1\u306e\u81e8\u5e8a\u90e8\u9580\u5168\u4f53\u3067\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u3066\u3044\u308b\u306e\u304b\u3001\u304a\u805e\u304b\u305b\u304f\u3060\u3055\u3044\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u554f\u984c\u306f\u3001\u767b\u9332\u3059\u308b\u60a3\u8005\u306b\u3064\u3044\u3066\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u3066\u3044\u308b\u304b\u3001\u3053\u306eAMKD\u96c6\u56e3\u306e\u30d9\u30fc\u30b9\u30e9\u30a4\u30f3\u7279\u6027\u306f\u3069\u306e\u3088\u3046\u306a\u3082\u306e\u3060\u3068\u8003\u3048\u3066\u3044\u308b\u304b\u3068\u3044\u3046\u3053\u3068\u3067\u3059\u3002\u7b2c2\/3\u76f8\u8a66\u9a13\u306e\u7d71\u4e00\u3055\u308c\u305f\u53c2\u52a0\u57fa\u6e96\u306f\u3001\u91cd\u8981\u306a\u57fa\u6e96\u3068\u3044\u3046\u610f\u5473\u3067\u3001\u5b9f\u306b3\u3064\u3042\u308a\u307e\u3059\u30021\u3064\u76ee\u306f\u3001APOL1\u5bfe\u7acb\u907a\u4f1d\u5b50\u304c2\u3064\u3042\u308b\u3053\u3068\u30022\u3064\u76ee\u306f\u3001\u814e\u6a5f\u80fd\u304c\u4f4e\u4e0b\u3057\u3066\u3044\u308b\u3053\u3068\u3002<\/p>\n<p>3\u3064\u76ee\u306f\u30010.7g\u3092\u8d85\u3048\u308b\u30bf\u30f3\u30d1\u30af\u5c3f\u3067\u3059\u3002\u3067\u3059\u304b\u3089\u3001\u3053\u306e\u8a66\u9a13\u306b\u53c2\u52a0\u3059\u308b\u3059\u3079\u3066\u306e\u60a3\u8005\u3055\u3093\u306f\u3001\u3053\u308c\u3089\u306e\u91cd\u8981\u306a\u57fa\u6e96\u3092\u6e80\u305f\u3059\u3053\u3068\u306b\u306a\u308a\u307e\u3059\u3002\u3082\u3061\u308d\u3093\u3001\u3054\u6307\u6458\u306e\u3088\u3046\u306b\u75be\u60a3\u306b\u306f\u5e45\u304c\u3042\u308a\u307e\u3059\u304b\u3089\u3001\u30bf\u30f3\u30d1\u30af\u5c3f\u306e\u7bc4\u56f2\u3084\u814e\u6a5f\u80fd\u306b\u95a2\u3057\u3066\u3082\u3001\u60a3\u8005\u3055\u3093\u306b\u306f\u591a\u69d8\u6027\u304c\u3042\u308b\u3053\u3068\u304c\u4e88\u60f3\u3055\u308c\u307e\u3059\u3002\u3057\u304b\u3057\u3001\u672c\u5f53\u306b\u91cd\u8981\u306a\u30dd\u30a4\u30f3\u30c8\u306f\u30012\u3064\u306eAPOL1\u5bfe\u7acb\u907a\u4f1d\u5b50\u3001\u30bf\u30f3\u30d1\u30af\u5c3f\u3001\u814e\u6a5f\u80fd\u4f4e\u4e0b\u3068\u3044\u3046\u3001\u3080\u3057\u308d\u5747\u8cea\u306a\u96c6\u56e3\u3067\u3042\u308b\u3068\u3044\u3046\u3053\u3068\u3067\u3059\u3002<\/p>\n<p>Lyla Youssef &#8212; Cowen and Company &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3002\u3068\u3066\u3082\u53c2\u8003\u306b\u306a\u308a\u307e\u3059\u3002\u305d\u3057\u3066\u3001\u3082\u3057\u3088\u308d\u3057\u3051\u308c\u3070\u3001\u3042\u306a\u305f\u304c\u304a\u3063\u3057\u3083\u3063\u305f\u3001\u767b\u9332\u4e2d\u306e\u89b3\u5bdf\u7814\u7a76\u306e\u30c7\u30fc\u30bf\u3092\u767a\u8868\u3055\u308c\u308b\u53ef\u80fd\u6027\u306f\u3042\u308a\u307e\u3059\u304b\uff1f\u30b8\u30a7\u30ce\u30bf\u30a4\u30d4\u30f3\u30b0\u30c7\u30fc\u30bf\u306a\u3069\u3092\u5f97\u308b\u305f\u3081\u3060\u3051\u3067\u3059\u304b\uff1f<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u3048\u3048\u3001\u3059\u3070\u3089\u3057\u3044\u8cea\u554f\u3067\u3059\u306d\u3002\u30c1\u30fc\u30e0\u5185\u3067\u305d\u306e\u30c7\u30fc\u30bf\u3092\u5171\u6709\u3059\u308b\u4e88\u5b9a\u3060\u3068\u601d\u3044\u307e\u3059\u3002\u3053\u306e\u7814\u7a76\u306f\u3001\u30b8\u30a7\u30ce\u30bf\u30a4\u30d4\u30f3\u30b0\u3092\u884c\u3046\u975e\u5e38\u306b\u30b7\u30f3\u30d7\u30eb\u306a\u89b3\u5bdf\u7814\u7a76\u306a\u306e\u3067\u3001\u3059\u3067\u306b\u30b9\u30af\u30ea\u30fc\u30cb\u30f3\u30b0\u3057\u3066\u767b\u9332\u3057\u305f\u60a3\u8005\u3055\u3093\u306e\u6570\u306f\u6570\u767e\u4eba\u306b\u9054\u3057\u3066\u3044\u307e\u3059\u3002IR\u30c1\u30fc\u30e0\u304c\u30aa\u30d5\u30e9\u30a4\u30f3\u3067\u8a73\u7d30\u3092\u6559\u3048\u3066\u304f\u308c\u308b\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>Lyla Youssef &#8212; \u30b3\u30fc\u30a6\u30a7\u30f3\u30a2\u30f3\u30c9\u30ab\u30f3\u30d1\u30cb\u30fc &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u308f\u304b\u308a\u307e\u3057\u305f\u3002\u7d20\u6674\u3089\u3057\u3044\u3002\u672c\u5f53\u306b\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u3001Evercore ISI\u306eLiisa Bayko\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Liisa Bayko &#8212; Evercore ISI &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3002SKYLINE 102\u304a\u3088\u3073103\u8a66\u9a13\u306b\u3064\u3044\u3066\u3001\u5177\u4f53\u7684\u306b\u4f55\u3092\u6c42\u3081\u3066\u3044\u308b\u306e\u304b\u3001\u305d\u308c\u306b\u7d9a\u304f\u611f\u899a\u3092\u6559\u3048\u3066\u3044\u305f\u3060\u3051\u308c\u3070\u3068\u601d\u3044\u307e\u3059\u3002\u30d9\u30f3\u30c1\u30de\u30fc\u30af\u3084\u81e8\u5e8a\u7684\u610f\u7fa9\u306f\u3069\u306e\u3088\u3046\u306a\u3082\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u3082\u3061\u308d\u3093\u3067\u3059\u3001Liisa\u3002SKYLINE &#8212; 2\u3064\u306eSKYLINE\u8a66\u9a13\u3068\u3001\u73fe\u5728\u9032\u884c\u4e2d\u306eRIDGELINE\u8a66\u9a13\u3001\u3064\u307e\u308a6\u6b73\u304b\u308911\u6b73\u3092\u5bfe\u8c61\u3068\u3057\u305f121\/561 tezacaftor\u306e\u8a66\u9a13\u3067\u3059\u304c\u3001\u3053\u3061\u3089\u3082\u9032\u884c\u4e2d\u3067\u3059\u3002HBE\u30a2\u30c3\u30bb\u30a4\u3092\u542b\u3080\u3059\u3079\u3066\u306e\u30c7\u30fc\u30bf\u306b\u57fa\u3065\u3044\u3066\u3001\u79c1\u305f\u3061\u304c\u6c42\u3081\u3066\u3044\u308b\u3053\u3068\u306f\u6b21\u306e\u3068\u304a\u308a\u3067\u3059\u3002<\/p>\n<p>\u6c57\u306e\u5869\u5316\u7269\u306f\u3001TRIKAFTA\u3088\u308a\u3082\u591a\u304f\u306a\u308b\u3068\u4e88\u60f3\u3057\u3066\u3044\u307e\u3059\u3002\u6c57\u306e\u5869\u5316\u7269\u3068ppFEV1\u3092\u8abf\u3079\u305f\u7b2c2\u76f8\u8a66\u9a13\u306b\u57fa\u3065\u3044\u3066\u3001121\/561 tez\u306fTRIKAFTA\u3088\u308a\u3055\u3089\u306b\u9ad8\u3044\u53ef\u80fd\u6027\u3092\u6301\u3063\u3066\u3044\u308b\u3068\u4e88\u60f3\u3057\u3066\u3044\u307e\u3059\u3002\u305d\u3057\u3066\u3001\u6700\u7d42\u7684\u306b\u79c1\u305f\u3061\u304c\u672c\u5f53\u306b\u6c42\u3081\u3066\u3044\u308b\u306e\u306f\u3001ppFEV1\u3001\u6c57\u306e\u5869\u5316\u7269\u6fc3\u5ea6\u3001\u305d\u3057\u3066\u3082\u3061\u308d\u3093\u3001\u5b89\u5168\u6027\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u306a\u306e\u3067\u3059\u3002\u524d\u81e8\u5e8a\u8a66\u9a13\u3068\u7b2c2\u76f8\u8a66\u9a13\u306e\u7d50\u679c\u304b\u3089\u3001121\/561 tez\u306fTRIKAFTA\u3088\u308a\u512a\u308c\u3066\u3044\u308b\u53ef\u80fd\u6027\u304c\u3042\u308b\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>CFTR\u30e2\u30b8\u30e5\u30ec\u30fc\u30bf\u30fc\u306e\u6a5f\u80fd\u3092\u77e5\u308b\u306b\u306f\u3001\u6c57\u306e\u5869\u5316\u7269\u3092\u898b\u308b\u306e\u304c\u4e00\u756a\u308f\u304b\u308a\u3084\u3059\u3044\u3093\u3067\u3059\u3002\u3053\u308c\u306f\u6700\u3082\u76f4\u63a5\u7684\u306a\u8aad\u307f\u51fa\u3057\u3001\u3044\u308f\u3070PD\u306e\u8aad\u307f\u51fa\u3057\u3067\u3059\u3002HBE\u3001\u7b2c1\u76f8\u8a66\u9a13\u3001\u7b2c2\u76f8\u8a66\u9a13\u306b\u304a\u3044\u3066\u3001\u3053\u306e\u65b9\u6cd5\u306f\u4e00\u8cab\u3057\u3066\u512a\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>Liisa Bayko &#8212; Evercore ISI &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u30d0\u30f3\u30af\u30fb\u30aa\u30d6\u30fb\u30a2\u30e1\u30ea\u30ab\u306eGeoff Meacham\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Geoff Meacham &#8212; \u30d0\u30f3\u30af\u30aa\u30d6\u30a2\u30e1\u30ea\u30ab\u30fb\u30e1\u30ea\u30eb\u30ea\u30f3\u30c1 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3001\u7686\u3055\u3093\u3002\u3054\u8cea\u554f\u3092\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u307e\u305f\u3001\u597d\u8abf\u306a\u56db\u534a\u671f\u306b\u304a\u3081\u3067\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002548\u306b\u3064\u3044\u3066\u304a\u805e\u304d\u3057\u305f\u3044\u306e\u3067\u3059\u304c\u3002<\/p>\n<p>\u5e02\u5834\u6a5f\u4f1a\u3068\u304b\u306a\u308a\u5e83\u7bc4\u306a\u30d7\u30ed\u30b0\u30e9\u30e0\u3092\u8003\u616e\u3057\u305f\u5834\u5408\u3001\u6210\u529f\u3068\u306f\u3069\u306e\u3088\u3046\u306a\u3082\u306e\u306a\u306e\u304b\u3001\u9ad8\u3044\u30ec\u30d9\u30eb\u3067\u3042\u306a\u305f\u306e\u898b\u89e3\u3092\u304a\u805e\u304b\u305b\u304f\u3060\u3055\u3044\u3002\u305d\u308c\u304b\u3089\u3001FDA\u3068\u306e\u30d7\u30ec\u30d5\u30a7\u30fc\u30ba3\u306e\u30df\u30fc\u30c6\u30a3\u30f3\u30b0\u304c\u3042\u3063\u305f\u304b\u3069\u3046\u304b\u308f\u304b\u308a\u307e\u305b\u3093\u304c\u3001\u4eca\u5e74\u306e\u5f8c\u534a\u306b\u958b\u59cb\u3059\u308b\u30d4\u30dc\u30bf\u30eb\u306e\u30b5\u30a4\u30ba\u3068\u7bc4\u56f2\u306b\u3064\u3044\u3066\u3069\u306e\u3088\u3046\u306b\u304a\u8003\u3048\u3067\u3057\u3087\u3046\u304b\uff1f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>Geoff\u3001\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u30ec\u30b7\u30e5\u30de\u3067\u3059\u3002\u307e\u305a\u306f\u79c1\u304b\u3089\u3001\u305d\u3057\u3066\u5e02\u5834\u6a5f\u4f1a\u306b\u3064\u3044\u3066\u306fStuart\u306b\u30d0\u30c8\u30f3\u30bf\u30c3\u30c1\u3057\u307e\u3059\u3002\u3053\u308c\u306f\u79c1\u304c\u975e\u5e38\u306b\u71b1\u610f\u3092\u3082\u3063\u3066\u53d6\u308a\u7d44\u3093\u3067\u3044\u308b\u30d7\u30ed\u30b0\u30e9\u30e0\u306e1\u3064\u3067\u3001\u79c1\u305f\u3061\u306f&#8230;\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u5927\u304d\u306a\u671f\u5f85\u3092\u5bc4\u305b\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u305d\u306e\u7406\u7531\u306f\u3001\u907a\u4f1d\u5b50\u3068\u85ac\u7406\u5b66\u7684\u306a\u691c\u8a3c\u306b\u3064\u3044\u3066\u306f\u3059\u3067\u306b\u304a\u8a71\u3057\u307e\u3057\u305f\u304c\u3001\u3082\u3046\u4e00\u3064\u306e\u7406\u7531\u306f\u3001\u6025\u6027\u75db\u3001\u795e\u7d4c\u5f62\u6210\u6027\u75db\u3001\u305d\u3057\u3066\u7b4b\u9aa8\u683c\u7cfb\u75db\u3068\u3067\u3082\u8a00\u3044\u307e\u3057\u3087\u3046\u304b\u3001\u672c\u5f53\u306b\u3042\u3089\u3086\u308b\u75db\u307f\u306b\u5bfe\u5fdc\u3067\u304d\u308b\u53ef\u80fd\u6027\u3092\u6301\u3063\u3066\u3044\u308b\u304b\u3089\u3067\u3059\u3002\u79c1\u304c\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u8208\u596e\u3059\u308b\u6700\u5f8c\u306e\u7406\u7531\u306f\u3001\u5e02\u5834\u6a5f\u4f1a\u304c\u77ed\u671f\u9593\u3067\u3042\u308b\u3053\u3068\u3067\u3059\u3002\u305d\u308c\u3067\u306f\u3001\u3053\u306e\u91cd\u8981\u306a\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u3044\u3066\u8aac\u660e\u3057\u307e\u3059\u3002\u305d\u3046\u305d\u3046\u3001FDA\u3068\u306e\u7b2c2\u76f8\u7d42\u4e86\u30df\u30fc\u30c6\u30a3\u30f3\u30b0\u304c\u7d42\u4e86\u3057\u3001\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u3044\u3066\u5408\u610f\u306b\u9054\u3057\u307e\u3057\u305f\u3002<\/p>\n<p>\u3053\u308c\u304c\u305d\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u3067\u3059\u30022,000\u4eba\u307b\u3069\u306e\u60a3\u8005\u3055\u3093\u3092\u5bfe\u8c61\u306b\u3001\u7b2c2\u76f8\u8a66\u9a13\u3068\u307e\u3063\u305f\u304f\u540c\u3058\u3088\u3046\u306b\u3001\u8179\u58c1\u5f62\u6210\u8853\u3068\u6241\u6843\u6458\u51fa\u8853\u306e2\u3064\u306e\u7121\u4f5c\u70ba\u5316\u6bd4\u8f03\u8a66\u9a13\u3092\u884c\u3044\u307e\u3059\u3002\u307e\u305f\u30013\u756a\u76ee\u306e\u30b7\u30f3\u30b0\u30eb\u30a2\u30fc\u30e0\u8a66\u9a13\u3067\u306f\u3001\u9aa8\u6298\u3084\u637b\u632b\u3001\u8edf\u7d44\u7e54\u640d\u50b7\u3060\u3051\u3067\u306a\u304f\u3001\u624b\u8853\u306b\u95a2\u9023\u3057\u305f\u3042\u3089\u3086\u308b\u7a2e\u985e\u306e\u75db\u307f\u3092\u5bfe\u8c61\u3068\u3057\u307e\u3059\u3002\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u3001\u4e2d\u7b49\u5ea6\u304b\u3089\u91cd\u5ea6\u306e\u75db\u307f\u306b\u5bfe\u3057\u3066\u3001\u5e45\u5e83\u3044\u6025\u6027\u75db\u306e\u9069\u5fdc\u3092\u6301\u3064\u3088\u3046\u306b\u8a2d\u8a08\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u305d\u308c\u304c\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u7d20\u6674\u3089\u3057\u3044\u3068\u3053\u308d\u3067\u3059\u3002<\/p>\n<p>\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u3001\u5e02\u5834\u306e\u53ef\u80fd\u6027\u306b\u3064\u3044\u3066\u306f\u3001\u3042\u306a\u305f\u306b\u5f15\u304d\u7d99\u304e\u307e\u3059\u3002<\/p>\n<p>Stuart Arbuckle &#8212; \u6700\u9ad8\u57f7\u884c\u8cac\u4efb\u8005\uff08COO<\/p>\n<p>\u306f\u3044\u3001Geoff\u3067\u3059\u3002\u79c1\u305f\u3061\u304cFDA\u3068\u306e\u5408\u610f\u306b\u8208\u596e\u3057\u3001\u7814\u7a76\u304c\u3046\u307e\u304f\u3044\u3051\u3070\u5e45\u5e83\u3044\u9069\u5fdc\u75c7\u306b\u3064\u306a\u304c\u308b\u53ef\u80fd\u6027\u304c\u3042\u308a\u3001\u305d\u308c\u306f\u79c1\u305f\u3061\u304c\u9ad8\u3044\u30ec\u30d9\u30eb\u3067\u78ba\u4fe1\u3057\u3066\u3044\u308b\u3053\u3068\u3067\u3059\u304c\u3001\u4e2d\u7b49\u5ea6\u304b\u3089\u91cd\u5ea6\u306e\u6025\u6027\u75db\u306e\u5e02\u5834\u304c\u975e\u5e38\u306b\u5927\u304d\u3044\u304b\u3089\u306a\u306e\u3067\u3059\u3002\u6e96\u5099\u66f8\u9762\u3067\u3082\u7533\u3057\u4e0a\u3052\u307e\u3057\u305f\u304c\u3001\u7c73\u56fd\u3060\u3051\u3067\u3082\u5e74\u959315\u5104\u65e5\u4ee5\u4e0a\u306eB\u578b\u6cbb\u7642\u304c\u884c\u308f\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u305d\u306e\u3046\u3061\u306e3\u5206\u306e2\u306e10\u5104\u65e5\u306f\u3001\u5165\u9662\u307e\u305f\u306f\u5916\u6765\u3067\u75db\u307f\u306e\u6cbb\u7642\u3092\u53d7\u3051\u305f\u60a3\u8005\u304c\u9000\u9662\u3059\u308b\u969b\u306b\u3001\u75c5\u9662\u3067\u6cbb\u7642\u304c\u958b\u59cb\u3055\u308c\u308b\u304b\u3001\u75c5\u9662\u304c\u5f71\u97ff\u3092\u4e0e\u3048\u308b\u3082\u306e\u306a\u306e\u3067\u3059\u3002\u3067\u3059\u304b\u3089\u300115\u5104\u65e5\u306e\u6cbb\u7642\u65e5\u6570\u306f\u3001\u3054\u5b58\u77e5\u306e\u3088\u3046\u306b\u3001\u305d\u306e\u5e02\u5834\u306e\u5927\u90e8\u5206\u304c\u73fe\u5728\u30b8\u30a7\u30cd\u30ea\u30c3\u30af\u5316\u3055\u308c\u3066\u3044\u307e\u3059\u3002\u3057\u304b\u3057\u3001\u305d\u308c\u3067\u3082\u4eca\u65e5\u3001\u7c73\u56fd\u3060\u3051\u306740\u5104\u30c9\u30eb\u306e\u5e02\u5834\u898f\u6a21\u304c\u3042\u308a\u307e\u3059\u3002<\/p>\n<p>\u3067\u3059\u304b\u3089\u3001\u5b89\u5168\u6027\u3068\u5fcd\u5bb9\u6027\u306e\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u306b\u512a\u308c\u305f\u3001\u52b9\u679c\u306e\u9ad8\u3044\u93ae\u75db\u5264\u3092\u5e02\u5834\u306b\u51fa\u305b\u3070\u3001\u305d\u308c\u306a\u308a\u306e\u30b7\u30a7\u30a2\u304c\u671f\u5f85\u3067\u304d\u3001\u3055\u3089\u306b1\u65e510\u30c9\u30eb\u7a0b\u5ea6\u306e\u4fa1\u683c\u306e\u7d4c\u53e3\u93ae\u75db\u5264\u306e\u30d6\u30e9\u30f3\u30c9\u5316\u3082\u671f\u5f85\u3067\u304d\u308b\u306f\u305a\u3060\u3068\u8003\u3048\u3066\u3044\u307e\u3059\u3002\u3053\u308c\u306f\u6570\u5341\u5104\u30c9\u30eb\u898f\u6a21\u306e\u975e\u5e38\u306b\u5927\u304d\u306a\u30c1\u30e3\u30f3\u30b9\u3067\u3059\u3002\u3060\u304b\u3089\u3053\u305d\u3001Reshma\u3082\u79c1\u3082\u3053\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u9ad8\u3044\u30ec\u30d9\u30eb\u306e\u71b1\u610f\u3092\u3082\u3063\u3066\u3044\u308b\u306e\u3067\u3059\u3002<\/p>\n<p>Geoff Meacham &#8212; Bank of America Merrill Lynch &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u308f\u304b\u308a\u307e\u3057\u305f\u3002\u3042\u308a\u304c\u3068\u3046\u3001\u307f\u3093\u306a\u3002<\/p>\n<p>\u53f8\u4f1a<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306fBMO\u30ad\u30e3\u30d4\u30bf\u30eb\u30de\u30fc\u30b1\u30c3\u30c4\u306e\u30a8\u30f4\u30a1\u30f3\u30fb\u30bb\u30a4\u30ac\u30de\u30f3\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>\u30a8\u30f4\u30a1\u30f3\u30fb\u30bb\u30a4\u30ac\u30fc\u30de\u30f3 &#8212; BMO\u30ad\u30e3\u30d4\u30bf\u30eb\u30fb\u30de\u30fc\u30b1\u30c3\u30c4 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7686\u3055\u3093\u3001\u3053\u3093\u306b\u3061\u306f\u3002\u8cea\u554f\u3092\u304a\u53d7\u3051\u3044\u305f\u3060\u304d\u3001\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u56db\u534a\u671f\u6c7a\u7b97\u304a\u3081\u3067\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002Geoff\u306e\u75db\u307f\u306b\u95a2\u3059\u308b\u8cea\u554f\u306e\u7d9a\u304d\u3067\u3059\u3002<\/p>\n<p>\u4e00\u6b69\u4e0b\u304c\u3063\u3066\u3001\u6025\u6027\u75db\u6cbb\u7642\u306e\u67a0\u7d44\u307f\u306e\u4e2d\u3067548\u304c\u3069\u306e\u3088\u3046\u306b\u4f4d\u7f6e\u3065\u3051\u3089\u308c\u308b\u304b\u306b\u3064\u3044\u3066\u3001\u305c\u3072\u6559\u3048\u3066\u304f\u3060\u3055\u3044\u3002\u76ee\u6a19\u306f\u3001\u30aa\u30d4\u30aa\u30a4\u30c9\u7642\u6cd5\u306b\u5148\u884c\u3057\u3066548\u3092\u4f7f\u7528\u3059\u308b\u3053\u3068\u3060\u3068\u601d\u3044\u307e\u3059\u304c\u3001\u305d\u308c\u3067\u3082\u753b\u671f\u7684\u306a\u75db\u307f\u304c\u3042\u308b\u5834\u5408\u306f\u3001\u30aa\u30d4\u30aa\u30a4\u30c9\u7642\u6cd5\u3092\u9078\u629e\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u307e\u3059\u3002\u305d\u306e\u969b\u3001\u4e21\u8005\u3092\u4f75\u7528\u3057\u305f\u5834\u5408\u306e\u5b89\u5168\u6027\u306e\u89b3\u70b9\u306f\u5fc5\u8981\u3067\u3057\u3087\u3046\u304b\uff1f\u307e\u305f\u3001\u3053\u306e\u4f75\u7528\u7642\u6cd5\u3092\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u3066\u304a\u3089\u308c\u308b\u306e\u304b\u3001\u6559\u3048\u3066\u304f\u3060\u3055\u3044\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u30fb\u30a2\u30fc\u30d0\u30c3\u30af\u30eb &#8212; \u30c1\u30fc\u30d5\u30fb\u30aa\u30da\u30ec\u30fc\u30c6\u30a3\u30f3\u30b0\u30fb\u30aa\u30d5\u30a3\u30b5\u30fc<\/p>\n<p>\u306f\u3044\u3001\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u3067\u3059\u3002\u3053\u3061\u3089\u3082\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002\u73fe\u5728\u306e\u6025\u6027\u75db\u306e\u7ba1\u7406\u65b9\u6cd5\u306f\u3001\u660e\u3089\u304b\u306b\u3001\u975e\u5e38\u306b\u8efd\u5ea6\u3067\u3042\u308c\u3070\u3001\u5e02\u8ca9\u306e\u93ae\u75db\u5264\u3092\u670d\u7528\u3057\u3001\u305d\u306e\u5f8c\u3001\u975e\u30b9\u30c6\u30ed\u30a4\u30c9\u7cfb\u306b\u79fb\u884c\u3057\u3001\u30aa\u30d4\u30aa\u30a4\u30c9\u306b\u79fb\u884c\u3057\u3001\u3055\u3089\u306b\u4ed6\u306e\u3082\u306e\u306b\u79fb\u884c\u3057\u3066\u3044\u307e\u3059\u3002\u3064\u307e\u308a\u3001VX-548\u306f\u3001\u975e\u30b9\u30c6\u30ed\u30a4\u30c9\u7cfb\u93ae\u75db\u5264\u3068\u30aa\u30d4\u30aa\u30a4\u30c9\u306e\u9593\u306b\u4f4d\u7f6e\u3059\u308b\u30b9\u30c6\u30c3\u30d7\u30bb\u30e9\u30d4\u30fc\u306e\u3088\u3046\u306a\u3082\u306e\u306a\u306e\u3067\u3059\u3002<\/p>\n<p>\u305d\u3057\u3066\u3001\u3053\u308c\u307e\u3067\u306e\u81e8\u5e8a\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3084\u533b\u5e2b\u3068\u306e\u8a71\u3057\u5408\u3044\u304b\u3089\u3001\u3053\u306e\u3088\u3046\u306a\u85ac\u7269\u7642\u6cd5\u304c\u73fe\u5b9f\u7684\u306a\u63d0\u6848\u3067\u3042\u308b\u3068\u4fe1\u3058\u3066\u3044\u307e\u3059\u3002\u3067\u3059\u304b\u3089\u3001\u79c1\u305f\u3061\u304c\u3053\u308c\u307e\u3067\u898b\u3066\u304d\u305f\u6709\u52b9\u6027\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u3068\u5b89\u5168\u6027\u30fb\u5fcd\u5bb9\u6027\u30d7\u30ed\u30d5\u30a1\u30a4\u30eb\u306b\u57fa\u3065\u3044\u3066\u3001\u3053\u306e\u85ac\u304c\u6cbb\u7642\u306e\u30d1\u30e9\u30c0\u30a4\u30e0\u306b\u9069\u5408\u3059\u308b\u3068\u8003\u3048\u3066\u3044\u308b\u308f\u3051\u3067\u3059\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u30a8\u30f4\u30a1\u30f3\u3001\u30ec\u30b7\u30e5\u30de\u3067\u3059\u3002\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u304c\u8a00\u3063\u305f\u3053\u3068\u306b\u4ed8\u3051\u52a0\u3048\u308b\u3068\u3001\u3053\u306e\u56fd\u3067\u306f\u30aa\u30d4\u30aa\u30a4\u30c9\u304c\u731b\u70c8\u306b\u8513\u5ef6\u3057\u3066\u3044\u307e\u3059\u3002\u3053\u308c\u306f\u516c\u8846\u885b\u751f\u306e\u5371\u6a5f\u3067\u3059\u3002CDC\u306e\u6700\u65b0\u306e\u5831\u544a\u3067\u306f\u3001\u6628\u5e74\u306f7\u4e075,000\u4eba\u304c\u6b7b\u4ea1\u3057\u3001\u524d\u5e74\u6bd435\uff05\u5897\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u3067\u3059\u304b\u3089\u3001\u3053\u308c\u306f\u6b74\u53f2\u7684\u306a\u554f\u984c\u3067\u306f\u3042\u308a\u307e\u305b\u3093\u3002\u73fe\u5728\u306e\u5371\u6a5f\u306a\u306e\u3067\u3059\u3002\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u304c\u8ff0\u3079\u305f\u3088\u3046\u306b\u3001\u5e02\u8ca9\u306e\u93ae\u75db\u5264\u304b\u3089VX-548\u306e\u3088\u3046\u306a\u85ac\u7269\u3078\u3068\u6bb5\u968e\u3092\u8e0f\u3093\u3067\u3044\u304f\u30a2\u30d7\u30ed\u30fc\u30c1\u306f\u3001\u672b\u68a2\u306b\u3057\u304b\u4f5c\u7528\u3057\u306a\u3044\u305f\u3081\u3001\u4e2d\u67a2\u306e\u53d7\u5bb9\u4f53\u304c\u5b58\u5728\u3057\u306a\u3044\u306e\u3060\u3068\u601d\u3044\u307e\u3059\u3002\u3053\u306e\u85ac\u306b\u306f\u4e2d\u6bd2\u6027\u304c\u306a\u3044\u306e\u3067\u3001\u975e\u5e38\u306b\u5927\u304d\u306a\u53ef\u80fd\u6027\u3092\u6301\u3063\u3066\u3044\u308b\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>\u79c1\u305f\u3061\u304c\u8a71\u3092\u3057\u305f\u533b\u5e2b\u3084\u5730\u57df\u56e3\u4f53\u3001\u533b\u7642\u95a2\u4fc2\u8005\u304b\u3089\u306f\u3001\u3053\u306e\u7a2e\u306e\u30e1\u30ab\u30cb\u30ba\u30e0\u306b\u5927\u304d\u306a\u71b1\u610f\u304c\u5bc4\u305b\u3089\u308c\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u30a8\u30f4\u30a1\u30f3\u30fb\u30bb\u30a4\u30ac\u30fc\u30de\u30f3 &#8212; BMO\u30ad\u30e3\u30d4\u30bf\u30eb\u30de\u30fc\u30b1\u30c3\u30c4 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306fUBS\u306eColin Bristow\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Colin Bristow &#8212; UBS &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3001\u56db\u534a\u671f\u6c7a\u7b97\u304a\u3081\u3067\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002Viacyte\u306e\u8cb7\u53ce\u306b\u3064\u3044\u3066\u3001VX-880\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u3044\u3066\u3067\u3059\u3002\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u91cd\u8907\u90e8\u5206\u304c\u3042\u308b\u3053\u3068\u306f\u660e\u3089\u304b\u3067\u3059\u3002\u512a\u5148\u9806\u4f4d\u4ed8\u3051\u306f\u3069\u306e\u3088\u3046\u306b\u8003\u3048\u308c\u3070\u3088\u3044\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u307e\u305f\u3001\u30d7\u30ed\u30b0\u30e9\u30e0\u5168\u4f53\u3092\u3069\u306e\u3088\u3046\u306b\u88dc\u5f37\u3057\u3066\u3044\u308b\u306e\u304b\u3001\u3082\u3046\u5c11\u3057\u8a73\u3057\u304f\u6559\u3048\u3066\u304f\u3060\u3055\u3044\u3002VX-548\u306b\u3064\u3044\u3066\u306f\u3001\u5e74\u5185\u306b\u81e8\u5e8a\u8a66\u9a13\u3092\u958b\u59cb\u3059\u308b\u3088\u3046\u3067\u3059\u304c\u3001\u6bcd\u96c6\u56e3\u898f\u6a21\u306f\u5927\u304d\u3044\u3082\u306e\u306e\u3001\u4e3b\u8981\u8a55\u4fa1\u9805\u76ee\u304c\u77ed\u3044\u3053\u3068\u3092\u8a8d\u8b58\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u3053\u308c\u3089\u306e\u8a66\u9a13\u306b\u3064\u3044\u3066\u3001\u3044\u3064\u3054\u308d\u30c8\u30c3\u30d7\u30e9\u30a4\u30f3\u3092\u767a\u8868\u3067\u304d\u308b\u72b6\u614b\u306b\u306a\u308b\u3068\u601d\u308f\u308c\u307e\u3059\u304b\uff1f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u30b3\u30ea\u30f3 \u6700\u521d\u306b548\u306e\u8cea\u554f\u306b\u53d6\u308a\u7d44\u307f\u3001\u305d\u306e\u5f8c\u3001Viacyte\u30681\u578b\u7cd6\u5c3f\u75c5\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u53d6\u308a\u7d44\u307f\u307e\u3059\u3002548\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u3001\u6975\u3081\u3066\u91cd\u8981\u306a\u30d7\u30ed\u30b0\u30e9\u30e0\u3067\u3059\u3002\u3053\u308c\u306f\u5b9f\u306b\u52b9\u7387\u7684\u306a\u958b\u767a\u30d7\u30ed\u30b0\u30e9\u30e0\u3067\u3059\u3002<\/p>\n<p>\u3053\u308c\u3089\u306e\u8a66\u9a13\u306f\u671f\u9593\u304c\u975e\u5e38\u306b\u77ed\u3044\u306e\u3067\u3059\u3002\u79c1\u305f\u3061\u306f\u3001\u305d\u306e\u65b9\u6cd5\u3092\u3088\u304f\u7406\u89e3\u3057\u3066\u3044\u307e\u3059\u3002VX-150\u3067\u3082\u305d\u3046\u3067\u3057\u305f\u3057\u3001VX-5\u3067\u3082\u305d\u3046\u3067\u3057\u305f\u3002VX-150\u3067\u5b9f\u65bd\u3057\u3001VX-548\u3067\u518d\u3073\u5b9f\u65bd\u3057\u307e\u3057\u305f\u3002<\/p>\n<p>\u305d\u3057\u3066\u3001RCT\uff08\u7121\u4f5c\u70ba\u5316\u81e8\u5e8a\u8a66\u9a13\uff09\u306f\u3001\u5916\u53cd\u6bcd\u8dbe\u5207\u9664\u8853\u3068\u8179\u90e8\u5f62\u6210\u8853\u3068\u3044\u3046\u3001\u975e\u5e38\u306b\u3088\u304f\u7406\u89e3\u3055\u308c\u3066\u3044\u308b\u624b\u8853\u65b9\u6cd5\u3067\u3059\u3002\u3053\u308c\u3089\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u8fc5\u901f\u306b\u9032\u5c55\u3059\u308b\u3068\u671f\u5f85\u3057\u3066\u3044\u307e\u3059\u3002\u30d0\u30a4\u30a2\u30b5\u30a4\u30c8\u793e\u306e\u8cb7\u53ce\u306b\u3064\u3044\u3066\u30021\u578b\u7cd6\u5c3f\u75c5\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u304a\u3051\u308b\u79c1\u305f\u3061\u306e\u771f\u306e\u76ee\u6a19\u306f\u3001\u3053\u306e\u75c5\u6c17\u3092\u6cbb\u3059\u3068\u307e\u3067\u306f\u3044\u304b\u306a\u3044\u307e\u3067\u3082\u3001\u5909\u3048\u3066\u3044\u304f\u3053\u3068\u3067\u3059\u3002<\/p>\n<p>\u305d\u308c\u304c\u79c1\u305f\u3061\u306e\u76ee\u6307\u3059\u3068\u3053\u308d\u3067\u3059\u3002VX-880\u3001\u3053\u308c\u306f\u88f8\u7d30\u80de\u30d7\u30ed\u30b0\u30e9\u30e0\u3068\u547c\u3093\u3067\u3044\u307e\u3059\u3002\u6b21\u306b\u3001VX-880\u3068\u540c\u3058\u7d30\u80de\u3092\u514d\u75ab\u7cfb\u3092\u56de\u907f\u3059\u308b\u305f\u3081\u306e\u88c5\u7f6e\u306b\u7d44\u307f\u8fbc\u3093\u3060\u30d7\u30ed\u30b0\u30e9\u30e0\u3002\u305d\u3057\u30663\u3064\u76ee\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u3001\u305d\u306e\u540c\u3058\u7d30\u80de\u3092\u7de8\u96c6\u3057\u3066\u3001\u4f4e\u514d\u75ab\u7d30\u80de\u3068\u547c\u3073\u307e\u3059\u3002<\/p>\n<p>VX-880\u3092\u534a\u91cf\u6295\u4e0e\u3057\u305f\u6700\u521d\u306e2\u4eba\u306e\u60a3\u8005\u304b\u3089\u308f\u304b\u308b\u3088\u3046\u306b\u3001\u79c1\u305f\u3061\u306f\u3053\u306e1\u578b\u7cd6\u5c3f\u75c5\u3092\u5909\u3048\u308b\u3068\u3044\u3046\u76ee\u6a19\u306e\u9054\u6210\u306b\u5411\u3051\u3066\u9806\u8abf\u306b\u9032\u3093\u3067\u3044\u308b\u306e\u3067\u3059\u3002\u79c1\u305f\u3061\u304c\u884c\u3063\u3066\u3044\u308b\u3053\u3068\u3001\u305d\u3057\u3066\u30d0\u30a4\u30a2\u30b5\u30a4\u30c8\u793e\u306e\u8cb7\u53ce\u306e\u4fa1\u5024\u306f\u3001\u3053\u306e\u76ee\u6a19\u3092\u9054\u6210\u3059\u308b\u80fd\u529b\u3092\u52a0\u901f\u3055\u305b\u308b\u3053\u3068\u3067\u3059\u3002\u5177\u4f53\u7684\u306b\u306f\u3001\u30d0\u30a4\u30a2\u30b5\u30a4\u30c8\u793e\u306f\u79c1\u305f\u3061\u306b\u30c4\u30fc\u30eb\u3084\u6280\u8853\u3001\u7279\u306b\u88fd\u9020\u306b\u304a\u3051\u308bIP\u80fd\u529b\u3001\u305d\u3057\u3066\u624d\u80fd\u3092\u3082\u305f\u3089\u3057\u3001\u3053\u306e\u6cbb\u7642\u6cd5\u3092\u5b9f\u73fe\u3059\u308b\u80fd\u529b\u3092\u52a0\u901f\u3055\u305b\u308b\u3053\u3068\u306b\u306a\u308a\u307e\u3059\u3002\u3053\u308c\u3092\u30c0\u30d6\u30eb\u30af\u30ea\u30c3\u30af\u3059\u308b\u3068\u3001GMP\u7d30\u80de\u682a\u3001GMP\u88fd\u9020\u3001\u30d0\u30a4\u30a2\u30b5\u30a4\u30c8\u793e\u306eCRISPR\u30b3\u30e9\u30dc\u30ec\u30fc\u30b7\u30e7\u30f3\u306b\u3088\u308b\u514d\u75ab\u4f4e\u4e0b\u7d30\u80de\u306b\u3088\u308b\u81e8\u5e8a\u6bb5\u968e\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u3078\u306e\u30a2\u30af\u30bb\u30b9\u3068\u3044\u3046\u3053\u3068\u304c\u308f\u304b\u308a\u307e\u3059\u3002<\/p>\n<p>\u305d\u3057\u3066\u3001CF\u3067\u884c\u3063\u305f\u3088\u3046\u306b\u3001\u79c1\u305f\u3061\u306e\u76ee\u6a19\u306f&#8211;\u305d\u3057\u3066\u3001\u79c1\u305f\u3061\u304c\u671f\u5f85\u3057\u3066\u3044\u308b\u3053\u3068\u306f\u3001\u8907\u6570\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u3092\u4e26\u884c\u3057\u3066\u9032\u3081\u3001\u305d\u306e\u4e2d\u304b\u3089\u6700\u9069\u306a\u3082\u306e\u3092\u9078\u3093\u3067\u5f8c\u671f\u958b\u767a\u30fb\u5546\u696d\u5316\u3092\u884c\u3046\u3053\u3068\u3067\u3059\u3002<\/p>\n<p>Colin Bristow &#8212; UBS &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3067\u3059\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u53f8\u4f1a<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u3001SVB\u8a3c\u5238\u306e\u30c7\u30d3\u30c3\u30c9\u30fb\u30e9\u30a4\u30b8\u30f3\u30ac\u30fc\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>\u30c7\u30fc\u30d3\u30c3\u30c9\u30fb\u30e9\u30a4\u30b8\u30f3\u30ac\u30fc &#8212; SVB\u8a3c\u5238 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3069\u3046\u3082\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002AMKD\u306e\u4e2d\u9593\u89e3\u6790\u306b\u3064\u3044\u3066\u3001\u3044\u304f\u3064\u304b\u8cea\u554f\u304c\u3042\u308a\u307e\u3059\u3002\u30b3\u30f3\u30c8\u30ed\u30fc\u30eb\u7fa4\u306e48\u9031\u6642\u70b9\u306eeGFR\u4f4e\u4e0b\u7387\u306e\u4e88\u60f3\u306b\u3064\u3044\u3066\u304a\u805e\u304b\u305b\u304f\u3060\u3055\u3044\u3002\u305d\u308c\u306f\u77ed\u671f\u9593\u3067\u3042\u308a\u3001\u30b3\u30f3\u30c8\u30ed\u30fc\u30eb\u7fa4\u306e\u60a3\u8005\u3055\u3093\u306f\u3001\u6a19\u6e96\u6cbb\u7642\u3067\u5341\u5206\u306b\u30b1\u30a2\u3055\u308c\u308b\u3068\u601d\u3044\u307e\u3059\u304c\u3001\u73fe\u5b9f\u306b\u306f\u305d\u3046\u3068\u306f\u9650\u308a\u307e\u305b\u3093\u3002<\/p>\n<p>\u3067\u3059\u304b\u3089\u3001\u30b3\u30f3\u30c8\u30ed\u30fc\u30eb\u7fa4\u306e\u6e1b\u5c11\u3092\u3069\u306e\u3088\u3046\u306b\u898b\u8fbc\u3093\u3067\u3044\u308b\u306e\u304b\u3001\u3054\u7406\u89e3\u3044\u305f\u3060\u3051\u308c\u3070\u3068\u601d\u3044\u307e\u3059\u3002\u305d\u308c\u304b\u3089\u3001\u4e2d\u9593\u5831\u544a\u3067\u30cf\u30f3\u30c9\u30ea\u30f3\u30b0\u306b\u6210\u529f\u3057\u305f\u3068\u4eee\u5b9a\u3057\u3066\u3001FDA\u306f\u80af\u5b9a\u7684\u306a\u4e2d\u9593\u30c7\u30fc\u30bf\u3060\u3051\u3067\u65e9\u671f\u7533\u8acb\u3092\u652f\u6301\u3059\u308b\u3088\u3046\u306a\u793a\u5506\u3092\u4e0e\u3048\u3066\u3044\u307e\u3059\u304b\uff1f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; 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Risinger &#8212; SVB\u8a3c\u5238 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u53f8\u4f1a<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u30a6\u30a7\u30eb\u30ba\u30fb\u30d5\u30a1\u30fc\u30b4\u306e\u30e2\u30d2\u30c3\u30c8\u30fb\u30d0\u30f3\u30b5\u30eb\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Mohit Bansal &#8212; Wells Fargo Securities &#8212; 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&#8212; \u6700\u9ad8\u8ca1\u52d9\u8cac\u4efb\u8005<\/p>\n<p>\u3082\u3061\u308d\u3093\u3067\u3059\u3001Mohit\u3002\u3044\u3044\u8cea\u554f\u3067\u3059\u306d\u3002\u5148\u307b\u3069\u7533\u3057\u4e0a\u3052\u305f\u3088\u3046\u306b\u3001\u6700\u8fd1\u306e\u30d1\u30a4\u30d7\u30e9\u30a4\u30f3\u306e\u6210\u529f\u306f\u524d\u4ee3\u672a\u805e\u306e\u3082\u306e\u3067\u3059\u3002\u5f53\u7136\u306a\u304c\u3089\u3001\u7d20\u6674\u3089\u3057\u3044\u30c7\u30fc\u30bf\u3068\u6570\u5341\u5104\u30c9\u30eb\u898f\u6a21\u306e\u30d3\u30b8\u30cd\u30b9\u30c1\u30e3\u30f3\u30b9\u304c\u3042\u308b\u305f\u3081\u3001\u5f53\u793e\u306f\u3053\u308c\u3089\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u306e\u6210\u529f\u306b\u5411\u3051\u3066\u6295\u8cc7\u3092\u884c\u3063\u3066\u304a\u308a\u3001\u3053\u308c\u304c\u6700\u8fd1\u306e\u56db\u534a\u671f\u3068\u30ac\u30a4\u30c0\u30f3\u30b9\u306b\u304a\u3051\u308bOPEX\u306e\u4e0a\u6607\u306e\u8981\u56e0\u3068\u306a\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u30ac\u30a4\u30c0\u30f3\u30b9\u306e\u4e2d\u3067\u7279\u306b\u5f37\u8abf\u3057\u305f\u3044\u306e\u306f\u3001\u30da\u30a4\u30f3\u3068AMKD\u306e\u6210\u529f\u304c\u3001\u7d4c\u8cbb\u30ac\u30a4\u30c0\u30f3\u30b9\u3092\u5909\u66f4\u3059\u308b\u6700\u5927\u306e\u8981\u56e0\u3067\u3042\u308b\u3068\u3044\u3046\u3053\u3068\u3067\u3059\u3002\u307e\u305f\u3001\u91cd\u8981\u306a\u3053\u3068\u306f\u3001\u5897\u52a0\u5206\u306e\u3059\u3079\u3066\u3001\u3064\u307e\u308a90%\u4ee5\u4e0a\u304c\u7814\u7a76\u958b\u767a\u8cbb\u3067\u3042\u308b\u3068\u3044\u3046\u3053\u3068\u3067\u3059\u3002\u3067\u3059\u304b\u3089\u3001\u79c1\u305f\u3061\u306e\u89b3\u70b9\u304b\u3089\u306f\u975e\u5e38\u306b\u826f\u3044\u30cb\u30e5\u30fc\u30b9\u3067\u3042\u308a\u3001\u4eca\u5f8c\u3082\u6295\u8cc7\u3092\u7d9a\u3051\u3066\u3044\u304f\u3064\u3082\u308a\u3067\u3059\u3002\u30de\u30fc\u30b8\u30f3\u3092\u7dad\u6301\u3059\u308b\u80fd\u529b\u3068\u3044\u3046\u70b9\u3067\u306f\u3001\u79c1\u305f\u3061\u306f\u7d20\u6674\u3089\u3057\u3044\u30e2\u30c7\u30eb\u3092\u6301\u3063\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>\u91cd\u7be4\u306a\u75be\u60a3\u306b\u5bfe\u3059\u308b\u9769\u65b0\u7684\u306a\u533b\u85ac\u54c1\u3092\u958b\u767a\u3059\u308b\u5834\u5408\u3001\u305d\u3053\u306b\u306f\u975e\u5e38\u306b\u5927\u304d\u306a\u4fa1\u5024\u304c\u3042\u308a\u3001\u305d\u306e\u305f\u3081\u306b\u79c1\u305f\u3061\u306f\u4e00\u8cab\u3057\u3066\u6280\u8853\u9769\u65b0\u306b\u518d\u6295\u8cc7\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u308b\u306e\u3067\u3059\u3002\u3053\u306e\u30e2\u30c7\u30eb\u306b\u3088\u308a\u3001\u5f53\u9762\u306f\u975e\u5e38\u306b\u9b45\u529b\u7684\u306a\u55b6\u696d\u5229\u76ca\u7387\u3092\u7dad\u6301\u3067\u304d\u308b\u3068\u8003\u3048\u3066\u3044\u307e\u3059\u3002\u30d0\u30a4\u30a2\u30b7\u30f3\u306b\u95a2\u3059\u308b\u3054\u8cea\u554f\u3067\u3059\u304c\u3001\u30d0\u30a4\u30a2\u30b7\u30f3\u306b\u3064\u3044\u3066\u306f\u3001\u307e\u3060\u30ac\u30a4\u30c0\u30f3\u30b9\u306e\u5bfe\u8c61\u306b\u306f\u306a\u3063\u3066\u3044\u307e\u305b\u3093\u3002\u30cf\u30fc\u30c8-\u30b9\u30b3\u30c3\u30c8-\u30ed\u30b8\u30ce\u306e\u5f85\u3061\u6642\u9593\u306b\u3042\u308a\u3001\u53d6\u5f15\u306e\u5b8c\u4e86\u65e5\u3092\u6b63\u78ba\u306b\u4e88\u6e2c\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u306a\u3044\u305f\u3081\u3001\u30ac\u30a4\u30c0\u30f3\u30b9\u306b\u306f\u542b\u307e\u308c\u3066\u3044\u307e\u305b\u3093\u3002<\/p>\n<p>\u3053\u308c\u306f\u30ac\u30a4\u30c0\u30f3\u30b9\u306b\u542b\u307e\u308c\u3066\u3044\u307e\u305b\u3093\u3002\u53d6\u5f15\u5b8c\u4e86\u65e5\u304c\u308f\u304b\u308a\u6b21\u7b2c\u3001\u9069\u5b9c\u66f4\u65b0\u3057\u3066\u3044\u304d\u307e\u3059\u3002<\/p>\n<p>Mohit Bansal &#8212; \u30a6\u30a7\u30eb\u30ba\u30fb\u30d5\u30a1\u30fc\u30b4\u8a3c\u5238 &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u30ab\u30f3\u30c8\u30fc\u30eb\u30fb\u30d5\u30a3\u30c3\u30c4\u30b8\u30a7\u30e9\u30eb\u30c9\u306e\u30aa\u30ea\u30d3\u30a2\u30fb\u30d6\u30ec\u30a4\u30e4\u30fc\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Olivia Brayer &#8212; Cantor Fitzgerald &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3002\u8cea\u554f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u305d\u3057\u3066\u7d20\u6674\u3089\u3057\u3044\u56db\u534a\u671f\u3092\u304a\u904e\u3054\u3057\u3067\u3059\u306d\u3002CTX001\u306b\u3064\u3044\u3066\u30d5\u30a9\u30ed\u30fc\u30a2\u30c3\u30d7\u3057\u305f\u3044\u3068\u601d\u3044\u307e\u3059\u3002FDA\u3068\u306e\u4ea4\u6e09\u4e2d\u3067\u3042\u308b\u3053\u3068\u306f\u627f\u77e5\u3057\u3066\u3044\u307e\u3059\u304c\u3001EMA\u3068MHRA\u304c\u5408\u610f\u3057\u305f\u7533\u8acb\u30d1\u30c3\u30b1\u30fc\u30b8\u3068\u7c73\u56fd\u3067\u7533\u8acb\u3057\u306a\u3051\u308c\u3070\u306a\u3089\u306a\u3044\u3082\u306e\u3068\u3067\u3001\u60a3\u8005\u6570\u3084\u8ffd\u8de1\u671f\u9593\u4ee5\u5916\u306b\u7570\u306a\u308b\u53ef\u80fd\u6027\u304c\u3042\u308b\u6307\u6a19\u306f\u3042\u308a\u307e\u3059\u304b\u3002<\/p>\n<p>\u305d\u308c\u304b\u3089\u3001\u7533\u8acb\u306b\u95a2\u3059\u308b\u7c21\u5358\u306a\u78ba\u8a8d\u4e8b\u9805\u3067\u3059\u3002\u30d7\u30ec\u30b9\u30ea\u30ea\u30fc\u30b9\u3067\u306f\u3001\u5e74\u672b\u307e\u3067\u306b\u6b27\u5dde\u3068\u82f1\u56fd\u3067\u7533\u8acb\u3059\u308b\u4e88\u5b9a\u3067\u3042\u308b\u3068\u8ff0\u3079\u3089\u308c\u3066\u3044\u307e\u3059\u304c\u3001\u7c73\u56fd\u306b\u3064\u3044\u3066\u306f\u7279\u306b\u8a00\u53ca\u3055\u308c\u3066\u3044\u307e\u305b\u3093\u3002\u305d\u3053\u3067\u3001\u524d\u63d0\u306b\u5909\u66f4\u304c\u306a\u3044\u304b\u3069\u3046\u304b\u3092\u78ba\u8a8d\u3057\u305f\u3044\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u3082\u3061\u308d\u3093\u3067\u3059\u3002\u79c1\u305f\u3061\u306f\u8a71\u3057\u5408\u3044\u3092\u7d9a\u3051\u3066\u304d\u307e\u3057\u305f\u3002\u79c1\u305f\u3061\u306f\u672c\u5f53\u306b\u5e78\u904b\u306a\u3053\u3068\u306b\u3001\u3053\u3061\u3089\u5074\u3068\u3042\u3061\u3089\u5074\u306e\u898f\u5236\u5f53\u5c40\u304b\u3089\u3042\u3089\u3086\u308b\u6307\u5b9a\u3092\u53d7\u3051\u3001\u5f7c\u3089\u3068\u983b\u7e41\u306b\u8a71\u3057\u5408\u3044\u3092\u3059\u308b\u3053\u3068\u304c\u53ef\u80fd\u3067\u3059\u3002MHRA\u3001EMA\u3001FDA\u3068\u306f\u4f55\u30ab\u6708\u3082\u8a71\u3057\u5408\u3044\u3092\u7d9a\u3051\u3066\u304d\u307e\u3057\u305f\u3002<\/p>\n<p>\u524d\u81e8\u5e8a\u8a66\u9a13\u306e\u30d1\u30c3\u30b1\u30fc\u30b8\u304c\u5b8c\u6210\u3059\u308b\u306b\u3064\u308c\u3001\u4f1a\u8a71\u306e\u5185\u5bb9\u3082\u5909\u5316\u3057\u3066\u304d\u307e\u3057\u305f\u3002CMC\u3084\u88fd\u9020\u3001\u305d\u306e\u4ed6\u3059\u3079\u3066\u306e\u30e2\u30b8\u30e5\u30fc\u30eb\u306b\u95a2\u3057\u3066\u3082\u89e3\u6c7a\u3057\u307e\u3057\u305f\u3002EMA\u3084MHRA\u3068\u306e\u8a71\u3057\u5408\u3044\u306f\u3001\u6700\u7d42\u7684\u306bFDA\u3068\u540c\u3058\u3088\u3046\u306a\u7d50\u8ad6\u306b\u9054\u3057\u307e\u3057\u305f\u3002\u305d\u308c\u306f\u3001\u7533\u8acb\u3059\u308b\u60a3\u8005\u6570\u3084\u30d5\u30a9\u30ed\u30fc\u30a2\u30c3\u30d7\u306e\u671f\u9593\u306b\u95a2\u3059\u308b\u3082\u306e\u3067\u3057\u305f\u3002<\/p>\n<p>\u79c1\u305f\u3061\u306f\u7d50\u8ad6\u306b\u9054\u3057\u307e\u3057\u305f\u3002\u79c1\u305f\u3061\u306f\u5408\u610f\u306b\u9054\u3057\u307e\u3057\u305f\u3002\u5f93\u3063\u3066\u3001\u9806\u8abf\u306b\u9032\u3093\u3067\u304a\u308a\u3001\u4eca\u5e74\u672b\u306b\u306f\u7533\u8acb\u3067\u304d\u308b\u3068\u8003\u3048\u3066\u3044\u307e\u3059\u3002FDA\u306b\u3064\u3044\u3066\u306f\u3001MHRA\u3084EMA\u306e\u3088\u3046\u306a\u30de\u30a4\u30eb\u30b9\u30c8\u30fc\u30f3\u306b\u307e\u3060\u5230\u9054\u3057\u3066\u3044\u306a\u3044\u3060\u3051\u3067\u3059\u3002<\/p>\n<p>\u60a3\u8005\u6570\u3084\u30d5\u30a9\u30ed\u30fc\u30a2\u30c3\u30d7\u306e\u671f\u9593\u306a\u3069\u306b\u3064\u3044\u3066\u306e\u8a71\u3057\u5408\u3044\u304c\u307e\u3060\u7d42\u308f\u3063\u3066\u3044\u306a\u3044\u3060\u3051\u3067\u3059\u3002\u4eca\u5f8c\u6570\u9031\u9593\u306e\u3046\u3061\u306b\u7d50\u8ad6\u3092\u51fa\u3059\u3068\u601d\u3044\u307e\u3059\u306e\u3067\u3001\u305d\u306e\u5f8c\u306b\u3054\u5831\u544a\u3057\u305f\u3044\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>Olivia Brayer &#8212; Cantor Fitzgerald &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3002\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u6b21\u306e\u8cea\u554f\u306f\u30aa\u30c3\u30da\u30f3\u30cf\u30a4\u30de\u30fc\u793e\u306eHartaj Singh\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Hartaj Singh &#8212; Oppenheimer and Company &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7d20\u6674\u3089\u3057\u3044\u3002\u8cea\u554f\u3092\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u672c\u5f53\u306b\u7d20\u6674\u3089\u3057\u3044\u56db\u534a\u671f\u3067\u3057\u305f\u3002Reshma\u30011\u5e74\u524d\u30012\u5e74\u524d\u306e\u8a18\u61b6\u306b\u3064\u3044\u3066\u5c11\u3057\u304a\u8a71\u3057\u307e\u3059\u304c\u3001AATD\u306f\u4eca\u5e74\u3001\u3055\u3089\u306b2\u3064\u306e\u5206\u5b50\u3092\u81e8\u5e8a\u306b\u5c0e\u5165\u3059\u308b\u3088\u3046\u3067\u3059\u306d\u3002<\/p>\n<p>\u4ee5\u524d\u3001\u3042\u306a\u305f\u306f\u3001\u3053\u308c\u3089\u306e\u5206\u5b50\u306e\u52b9\u80fd\u3092\u9ad8\u3081\u3001\u3088\u308a\u9ad8\u6fc3\u5ea6\u3067\u76ee\u7684\u306e\u7d44\u7e54\u306b\u4f5c\u7528\u3055\u305b\u3088\u3046\u3068\u3057\u3066\u3044\u308b\u3068\u304a\u3063\u3057\u3083\u3063\u3066\u3044\u307e\u3057\u305f\u3002\u4eca\u5e74\u3001\u3053\u308c\u3089\u306e\u5206\u5b50\u3092\u30af\u30ea\u30cb\u30c3\u30af\u306b\u5c0e\u5165\u3059\u308b\u305f\u3081\u306e\u30a2\u30d7\u30ed\u30fc\u30c1\u306b\u3064\u3044\u3066\u3001\u3069\u306e\u3088\u3046\u306b\u304a\u8003\u3048\u3067\u3059\u304b\uff1f\u307e\u305f\u3001\u4eca\u5e74\u4e2d\u306b\u81e8\u5e8a\u3067\u4f7f\u3048\u308b\u3088\u3046\u306b\u306a\u3063\u305f\u3068\u3057\u3066\u3001\u4eca\u5f8c\u3001\u3044\u3064\u3054\u308d\u8aad\u307f\u53d6\u308c\u308b\u3088\u3046\u306b\u306a\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u3054\u8cea\u554f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u3053\u3093\u306b\u3061\u306f\u3001Hartaj\u3067\u3059\u3002AATD\u30d7\u30ed\u30b0\u30e9\u30e0\u306b\u3064\u3044\u3066\u3067\u3059\u304c\u3001AATD\u306f\u4f9d\u7136\u3068\u3057\u3066\u95a2\u5fc3\u306e\u9ad8\u3044\u75be\u60a3\u3067\u3042\u308a\u3001Vertex\u306e\u6226\u7565\u306b\u3074\u3063\u305f\u308a\u306a\u75be\u60a3\u3067\u3059\u3002\u5c11\u306a\u304f\u3068\u30821\u3064\u306f\u4eca\u5e74\u4e2d\u306bIND\u3092\u53d6\u5f97\u3059\u308b\u3068\u601d\u3044\u307e\u3059\u304c\u3001\u3053\u306e\u6b21\u306e\u6ce2\u306b\u306f\u591a\u304f\u306e\u5206\u5b50\u30011\u3064\u4ee5\u4e0a\u306e\u5206\u5b50\u304c\u542b\u307e\u308c\u307e\u3059\u3002<\/p>\n<p>\u79c1\u305f\u3061\u306f\u3001\u52b9\u80fd\u3092\u9ad8\u3081\u308b\u3053\u3068\u304c\u3067\u304d\u307e\u3057\u305f\u3002\u6295\u4e0e\u91cf\u3082\u5c11\u306a\u3044\u3067\u3059\u3002\u6295\u4e0e\u91cf\u306e\u5e45\u3092\u5341\u5206\u306b\u691c\u8a0e\u3059\u308b\u3053\u3068\u306b\u306a\u308b\u3068\u601d\u3044\u307e\u3059\u3002\u305d\u3057\u3066\u3001\u6765\u5e74\u307e\u3067\u306b\u306f\u304a\u8a71\u3067\u304d\u308b\u3088\u3046\u306a\u7d50\u679c\u304c\u5f97\u3089\u308c\u308b\u3068\u671f\u5f85\u3057\u3066\u3044\u307e\u3059\u3002<\/p>\n<p>Hartaj\u306f\u3001\u3053\u306e\u75c5\u6c17\u306e\u80ba\u3068\u809d\u81d3\u306e\u4e21\u65b9\u306e\u75c7\u72b6\u306b\u53d6\u308a\u7d44\u3080\u3053\u3068\u304c\u91cd\u8981\u3067\u3042\u308b\u3053\u3068\u3092\u3001\u4ed6\u306e\u4eba\u306b\u3082\u4f1d\u3048\u3066\u3044\u307e\u3059\u3002\u3060\u304b\u3089\u3053\u305d\u3001\u4f4e\u5206\u5b50\u5316\u5408\u7269\u306e\u30a2\u30d7\u30ed\u30fc\u30c1\u306f\u79c1\u305f\u3061\u306b\u3068\u3063\u3066\u9b45\u529b\u7684\u3067\u3042\u308a\u3001\u305d\u306e\u8ffd\u6c42\u3092\u5207\u671b\u3057\u3066\u3044\u308b\u306e\u3067\u3059\u3002\u4ed6\u306e\u3059\u3079\u3066\u306e\u30a2\u30d7\u30ed\u30fc\u30c1\u306f\u3001\u5358\u306b\u75c5\u6c17\u306e\u4e21\u65b9\u306e\u75c7\u72b6\u306b\u5bfe\u51e6\u3059\u308b\u3082\u306e\u3067\u306f\u3042\u308a\u307e\u305b\u3093\u3002\u3057\u305f\u304c\u3063\u3066\u3001\u79c1\u306e\u8003\u3048\u3067\u306f\u3001\u3053\u306e\u30a2\u30d7\u30ed\u30fc\u30c1\u306b\u306f\u5909\u9769\u304c\u3042\u308a\u307e\u305b\u3093\u3002<\/p>\n<p>\u3067\u3059\u304b\u3089\u3001\u79c1\u305f\u3061\u304c\u6c42\u3081\u3066\u3044\u308b\u306e\u306f\u3001\u307e\u3055\u306b\u3053\u306e\u70b9\u306a\u306e\u3067\u3059\u3002\u6765\u5e74\u306b\u306f\u3001\u79c1\u305f\u3061\u5168\u54e1\u304c\u898b\u3066\u8a55\u4fa1\u3067\u304d\u308b\u3088\u3046\u306a\u7d50\u679c\u304c\u5f97\u3089\u308c\u308b\u306f\u305a\u3067\u3059\u3002<\/p>\n<p>Hartaj Singh &#8212; Oppenheimer and Company &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u3042\u308a\u304c\u3068\u3046\u3001Reshma\u3002\u3044\u308d\u3044\u308d\u306a\u60c5\u5831\u3092\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>\u30aa\u30da\u30ec\u30fc\u30bf\u30fc<\/p>\n<p>\u3082\u30461\u554f\u3001RBC\u30ad\u30e3\u30d4\u30bf\u30eb\u30fb\u30de\u30fc\u30b1\u30c3\u30c4\u306e\u30d6\u30e9\u30a4\u30a2\u30f3\u30fb\u30a2\u30d6\u30e9\u30cf\u30e0\u30ba\u304b\u3089\u3067\u3059\u3002\u3069\u3046\u305e\u3088\u308d\u3057\u304f\u304a\u9858\u3044\u3057\u307e\u3059\u3002<\/p>\n<p>Brian Abrahams &#8212; RBC Capital Markets &#8212; \u30a2\u30ca\u30ea\u30b9\u30c8<\/p>\n<p>\u7686\u3055\u3093\u3001\u6642\u9593\u3092\u5272\u3044\u3066\u3044\u305f\u3060\u3044\u3066\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002CTX001\u306e\u88fd\u9020\u3068\u4f9b\u7d66\u306b\u95a2\u3057\u3066\u3001\u3069\u306e\u3088\u3046\u306a\u72b6\u6cc1\u306b\u3042\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u6700\u8fd1\u3001\u30d6\u30ea\u30c3\u30b8\u30f3\u30b0\u30b9\u30bf\u30c7\u30a3\u3092\u6295\u7a3f\u3055\u308c\u307e\u3057\u305f\u306d\u3002\u305d\u308c\u304c\u6700\u7d42\u7684\u306b\u88fd\u9020\u306e\u62e1\u5927\u3068\u30b9\u30b1\u30fc\u30eb\u30a2\u30c3\u30d7\u306b\u3069\u306e\u3088\u3046\u306b\u5f79\u7acb\u3064\u306e\u304b\u8208\u5473\u304c\u3042\u308a\u307e\u3059\u3002\u307e\u305f\u3001\u305d\u308c\u306b\u95a2\u9023\u3057\u3066\u3001\u6b21\u4e16\u4ee3\u30ec\u30b8\u30e1\u30f3\u3084\u30b3\u30f3\u30c7\u30a3\u30b7\u30e7\u30cb\u30f3\u30b0\u30ec\u30b8\u30e1\u30f3\u306b\u95a2\u3057\u3066\u3001\u3053\u306e\u5206\u91ce\u3092\u3069\u306e\u3088\u3046\u306b\u898b\u3066\u304a\u3089\u308c\u307e\u3059\u304b\uff1f\u307e\u305f\u3001\u305d\u306e\u3088\u3046\u306a\u9577\u671f\u7684\u306a\u6a5f\u4f1a\u3092\u62e1\u5927\u3059\u308b\u305f\u3081\u306b\u3001\u3069\u306e\u7a0b\u5ea6\u5f79\u7acb\u3064\u53ef\u80fd\u6027\u304c\u3042\u308b\u306e\u3067\u3057\u3087\u3046\u304b\uff1f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3057\u305f\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u30d6\u30b9\u30eb\u30d5\u30a1\u30f3\u306e\u9577\u671f\u7684\u306a\u6a5f\u4f1a\u306b\u3064\u3044\u3066\u3001Stuart\u306b\u30b3\u30e1\u30f3\u30c8\u3057\u3066\u3082\u3089\u3044\u3001\u79c1\u306f\u623b\u3063\u3066\u88fd\u9020\u306b\u3064\u3044\u3066\u5c11\u3057\u304a\u8a71\u3057\u305f\u3044\u3068\u601d\u3044\u307e\u3059\u3002<\/p>\n<p>\u30b9\u30c1\u30e5\u30a2\u30fc\u30c8\u30fb\u30a2\u30fc\u30d0\u30c3\u30af\u30eb &#8212; \u6700\u9ad8\u57f7\u884c\u8cac\u4efb\u8005\uff08COO<\/p>\n<p>\u305d\u3046\u3067\u3059\u306d\u3002\u30d6\u30e9\u30a4\u30a2\u30f3\u3001\u3054\u8cea\u554f\u3042\u308a\u304c\u3068\u3046\u3054\u3056\u3044\u307e\u3059\u3002\u7c73\u56fd\u3068EU\u3067\u3001\u938c\u72b6\u8d64\u8840\u7403\u3068TDT\u3092\u5408\u308f\u305b\u308b\u3068\u3001\u938c\u72b6\u8d64\u8840\u7403\u3084\u03b2\u30b5\u30e9\u30bb\u30df\u30a2\u306e\u60a3\u8005\u3055\u3093\u306f\u7d0415\u4e07\u4eba\u3044\u308b\u3068\u601d\u308f\u308c\u307e\u3059\u3002<\/p>\n<p>\u6700\u521d\u306e\u4e0a\u5e02\u306f\u3001\u81e8\u5e8a\u8a66\u9a13\u306e\u5bfe\u8c61\u3068\u306a\u308b\u60a3\u8005\u3055\u3093\u3068\u540c\u69d8\u306b\u3001\u3088\u308a\u91cd\u75c7\u306e\u60a3\u8005\u3055\u3093\u3001\u73fe\u5728\u306e\u30d6\u30b9\u30eb\u30d5\u30a1\u30f3\u6cbb\u7642\u30ec\u30b8\u30e1\u30f3\u3067\u3053\u306e\u6cbb\u7642\u3092\u53d7\u3051\u308b\u3053\u3068\u3092\u691c\u8a0e\u3059\u308b\u53ef\u80fd\u6027\u306e\u3042\u308b\u60a3\u8005\u3055\u3093\u306b\u7126\u70b9\u3092\u5f53\u3066\u308b\u4e88\u5b9a\u3067\u3059\u3002\u305d\u306e\u6570\u306f\u304a\u305d\u3089\u304f\u7d0432,000\u4eba\u3067\u3001\u305d\u306e\u3046\u3061\u7d0425,000\u4eba\u306f\u938c\u72b6\u8d64\u8840\u7403\u75c7\u306e\u60a3\u8005\u3055\u3093\u3067\u3001\u305d\u306e\u5927\u534a\u306f\u7c73\u56fd\u306b\u3044\u307e\u3059\u3002\u3053\u308c\u304c\u6700\u521d\u306e\u4e0a\u5e02\u96c6\u56e3\u3067\u3059\u3002\u3082\u3057\u3001\u3088\u308a\u7a4f\u3084\u304b\u306a\u6cbb\u7642\u6cd5\u304c\u78ba\u7acb\u3055\u308c\u308c\u3070\u3001\u5916\u6765\u3067\u306e\u6cbb\u7642\u304c\u53ef\u80fd\u306b\u306a\u308b\u304b\u3082\u3057\u308c\u307e\u305b\u3093\u306d\u3002<\/p>\n<p>\u6280\u8853\u7684\u306a\u3053\u3068\u306fReshma\u304c\u30b3\u30e1\u30f3\u30c8\u3057\u3066\u304f\u308c\u308b\u3067\u3057\u3087\u3046\u3002\u3057\u304b\u3057\u3001\u30c1\u30e3\u30f3\u30b9\u3068\u3044\u3046\u610f\u5473\u3067\u306f\u300132,000\u4eba\u3092\u8d85\u3048\u3066150,000\u4eba\u307e\u3067\u5927\u5e45\u306b\u62e1\u5927\u3059\u308b\u3053\u3068\u304c\u3067\u304d\u308b\u3068\u601d\u3044\u307e\u3059\u3002\u5168\u90e8\u304c\u5168\u90e8\u305d\u3046\u3067\u306f\u306a\u3044\u304b\u3082\u3057\u308c\u307e\u305b\u3093\u304c\u3001\u304b\u306a\u308a\u62e1\u5927\u3059\u308b\u3053\u3068\u306f\u9593\u9055\u3044\u3042\u308a\u307e\u305b\u3093\u3002\u305d\u3046\u306a\u308c\u3070\u3001\u3088\u308a\u591a\u304f\u306e\u4eba\u304c\u624b\u8853\u3092\u53d7\u3051\u305f\u3044\u3068\u8003\u3048\u308b\u3088\u3046\u306b\u306a\u308b\u3067\u3057\u3087\u3046\u3002<\/p>\n<p>Reshma Kewalramani &#8212; \u6700\u9ad8\u7d4c\u55b6\u8cac\u4efb\u8005\u517c\u793e\u9577<\/p>\n<p>\u88fd\u9020\u306b\u95a2\u3057\u3066\u306f\u3001\u5168\u4f53\u304b\u3089\u898b\u308c\u3070\u3001\u4f8b\u3048\u3070CRISPR-Cas9\u3067\u53d6\u308a\u7d44\u307e\u308c\u3066\u3044\u308b\u4ed6\u306e\u75be\u60a3\u3088\u308a\u3082\u3001\u88fd\u9020\u306f\u5bb9\u6613\u306a\u8ab2\u984c\u3060\u3068\u601d\u3044\u307e\u3059\u3002\u3068\u3044\u3046\u306e\u3082\u3001\u3053\u308c\u306f\u751f\u4f53\u5916\u3067\u306e\u907a\u4f1d\u5b50\u7de8\u96c6\u3060\u304b\u3089\u3067\u3059\u3002\u305d\u3057\u3066\u3001\u672c\u8cea\u7684\u306b\u306f\u3001\u79c1\u305f\u3061\u304c\u8a71\u3057\u3066\u3044\u308b\u306e\u306f\u3001\u30ac\u30a4\u30c9RNA\u3068Cas9\u306e\u3053\u3068\u3067\u3059\u30022\u3064\u76ee\u306e\u30dd\u30a4\u30f3\u30c8\u306f\u3001CRISPR\u306e\u30d1\u30fc\u30c8\u30ca\u30fc\u306e\u304a\u304b\u3052\u3067\u3059\u304c\u3001\u79c1\u305f\u3061\u306f\u3053\u306e\u6cbb\u7642\u6cd5\u306e\u5546\u696d\u7684\u306a\u88fd\u9020\u306b\u3064\u3044\u3066\u3001\u6700\u521d\u304b\u3089\u8003\u3048\u3066\u3044\u305f\u3068\u3044\u3046\u3053\u3068\u3067\u3059\u3002<\/p>\n<p>\u3053\u308c\u306f\u30d7\u30ed\u30bb\u30b9\u958b\u767a\u3068\u3044\u3046\u610f\u5473\u3067\u306e\u8a71\u3067\u3059\u3002\u307e\u305f\u3001\u5b9f\u969b\u306e\u88fd\u9020\u73fe\u5834\u306b\u95a2\u3057\u3066\u3082\u305d\u3046\u3067\u3059\u3002\u81e8\u5e8a\u8a66\u9a13\u3067\u4f7f\u3063\u3066\u3044\u308b\u30d7\u30ed\u30bb\u30b9\u3068\u3001\u5546\u696d\u30d9\u30fc\u30b9\u3067\u4f7f\u3046\u30d7\u30ed\u30bb\u30b9\u306f\u57fa\u672c\u7684\u306b\u540c\u3058\u3067\u3059\u3002\u88fd\u9020\u62e0\u70b9\u3082\u307e\u3063\u305f\u304f\u540c\u3058\u3067\u3059\u3002<\/p>\n<p>\u3067\u3059\u304b\u3089\u3001CTX001\u306e\u5546\u696d\u751f\u7523\u306b\u3064\u3044\u3066\u306f\u3001\u672c\u5f53\u306b\u826f\u3044\u72b6\u614b\u306b\u3042\u308b\u3068\u611f\u3058\u3066\u3044\u307e\u3059\u3002\u305d\u3057\u3066\u3001\u79c1\u304c\u8a00\u3063\u305f\u3088\u3046\u306b\u3001\u751f\u4f53\u5916\u907a\u4f1d\u5b50\u7de8\u96c6\u3067\u3042\u308a\u3001Cas9\u3068\u30ac\u30a4\u30c9RNA\u3067\u3042\u308a\u3001\u305d\u308c\u3060\u3051\u306a\u306e\u3067\u3001\u7269\u4e8b\u306e\u5927\u7b4b\u3067\u306f\u3001\u3053\u308c\u306f\u3088\u308a\u7c21\u5358\u306a\u6311\u6226\u3067\u3059\u3002<\/p>\n<p>\u30d6\u30e9\u30a4\u30a2\u30f3\u30fb\u30a8\u30a4\u30d6\u30e9\u30cf\u30e0\u30ba 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border=\"0\"><\/a><br \/>\n<a href=\"https:\/\/stock.blogmura.com\/tenbagger\/ranking\/in?p_cid=11122923\" target=\"_blank\" rel=\"noopener\">\u306b\u307b\u3093\u30d6\u30ed\u30b0\u6751<\/a><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u30d0\u30fc\u30c6\u30c3\u30af\u30b9\u30fb\u30d5\u30a1\u30fc\u30de\u30b7\u30e5\u30fc\u30c6\u30a3\u30ab\u30eb\u30ba (VRTX)2022\u5e74\u7b2c2\u56db\u534a\u671f\u6c7a\u7b97\u8aac\u660e\u4f1a\u306e\u65e5\u672c\u8a9e\u8a33\u3067\u3059\u3002 \u58f2\u308a\u4e0a\u3052\u30fbEPS\u5171\u5e02\u5834\u4e88\u60f3\u3092\u4e0a\u56de\u3063\u3066\u304a\u308a\u30ac\u30a4\u30c0\u30f3\u30b9\u3082\u4e0a\u65b9\u4fee\u6b63\u3068\u826f\u3044\u611f\u3058\u3067\u3059\u306d\u3002 \u4eca\u5f8c\u306f\u30d0\u30a4\u30aa\u95a2\u9023\u304c\u6ce8\u76ee\u3055\u308c\u308b\u3068\u3082\u8a00\u308f\u308c\u3066 &#8230; 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